NCT04737460View on ClinicalTrials.gov

Study for the Treatment for CLN7 Disease

PHASE1Active, not recruitingINTERVENTIONAL

Enrollment

4

Participants

Timeline

Start Date

May 4, 2021

Primary Completion Date

February 1, 2028

Study Completion Date

February 1, 2029

Conditions

CLN7

Interventions

GENETIC

AAV9/CLN7

Enrollees will receive gene therapy via a viral vector

Trial Locations (1)

75390

Children' Health, Dallas

All Listed Sponsors

lead

Benjamin Greenberg

OTHER