115
Participants
Start Date
April 19, 2021
Primary Completion Date
July 31, 2026
Study Completion Date
July 31, 2026
Nusinersen
Administered as specified in the treatment arm
National Taiwan University Hospital, Taipei
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
Instituto Nacional de Pediatria, Mexico City
Hospital Infantil de Mexico Federico Gomez, Mexico City
Hospital Sant Joan de Deu, Esplugues Del Llobregat
King Faisal Specialist Hospital & Research Center, Riyadh
Tallinn Children's Hospital, Tallinn
Fondazione Serena Onlus - Centro Clinico Nemo, Milan
The Johns Hopkins Hospital, Baltimore
National Guard Health Affairs: King Abdulaziz Medical City, Jeddah
Hospital Universitario La Paz, Madrid
King Fahad Specialist Hospital, Dammam
Universitaetsklinikum Giessen und Marburg GmbH, Giessen
St. Jude Children's Research Hospital, Memphis
Antiguo Hospital Civil de Guadalajara Fray Antonio Alcalde, Guadalajara
Hospital Universitari i Politecnic La Fe, Valencia
Children's Medical Center, Plano
Universitaetsklinikum Freiburg, Freiburg im Breisgau
Children's Hospital Colorado, Aurora
Stanford University Medical Center, Sacramento
Peking University First Hospital, Beijing
Hospital Universitario San Ignacio, Bogotá
Russian Children Neuromuscular Center of Veltischev, Moskva
The Children's Hospital of Zhejiang University School of Medicine, Hangzhou
Guangzhou Woman and Children's Medical Center, Guangzhou
Regional Pediatric Clinical Hospital #1, Yekaterinburg
Hospital das Clinicas - FMUSP, São Paulo
Hospital Luis Calvo Mackenna, Santiago
Clinica Las Condes, Santiago
Clinica MEDS La Dehesa, Santiago
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Boston Children's Hospital, Boston
Hospital de Clínicas de Porto Alegre, Porto Alegre
London Health Sciences Centre (LHSC) - Children's Hospital, London
Kurume University Hospital, Kurume-shi
Hyogo Medical University Hospital, Nishinomiya-shi
Tokyo Women's Medical University Hospital, Shinjuku-ku
Saint George University Hospital Medical Center, Beirut
Lead Sponsor
Biogen
INDUSTRY