46
Participants
Start Date
December 14, 2020
Primary Completion Date
October 16, 2022
Study Completion Date
June 6, 2024
Lomitapide
2mg,5mg, 10mg and 20mg capsules
E.P.S. Fattouma Bourguiba Hospital, Monastir
Hospital Abente y Lago, A Coruña
University Medical Center Hamburg-Eppendorf, Hamburg
U.O.C. Clinica Medica 1, Padua
Hospital Universitari Sant Joan, Reus
Hospital Clinico Universitario of Valencia, Valencia
University Hospital of Cologne, Cologne
Chaim Sheba Medical Center, Ramat Gan
Universtiats-Kinderlinik Heidelberg, Heidelberg
Bambino Gesù Children's Hospital,, Roma
King Abdullah International Medical Research Centre (KAIMRC),, Riyadh
King Faisal Specialist Hospital, Riyadh
Lead Sponsor
Amryt Pharma
INDUSTRY