About
Orphan Specialty Drugs
Areas of Focus
Categories
Small Molecule Pharmaceutical
Clinical Trials (9)
View allTotal Trials
9
As Lead Sponsor
8
As Collaborator
1
Total Enrollment
1,046
By Phase
PHASE3: 4PHASE4: 1PHASE2: 1
By Status
RECRUITING: 5ACTIVE_NOT_RECRUITING: 2COMPLETED: 1TERMINATED: 1
Clinical Trials Pipeline9 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2013
2014
2015
2016
2017
2018
2019
2020
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
2032
2033
Today
Hover over trial bars to see details
Recent Trials
NCT06502990Lead Sponsor
Open-label Study to Evaluate Metreleptin in Children Under 6 Years of Age With Generalised Lipodystrophy
PHASE3Recruiting
15 participants
Started: May 23, 2025 · Completed: Sep 30, 2026
NCT06423573Lead Sponsor
A Study to Assess the Incidence of Skin Cancers in Patients With Epidermolysis Bullosa Receiving Filsuvez
N/ARecruiting
580 participants
Started: Dec 18, 2024 · Completed: Aug 1, 2032
NCT06679270Lead Sponsor
Open-label Extension Study to Evaluate Metreleptin in Patients With Partial Lipodystrophy
PHASE3Recruiting
15 participants
Started: Oct 14, 2024 · Completed: Mar 31, 2028
NCT06484868Lead Sponsor
Open-label Study to Evaluate Metreleptin in Patients With Partial Lipodystrophy
PHASE4Recruiting
12 participants
Started: Feb 8, 2024 · Completed: Feb 29, 2028
NCT05351164Collaborator
Evaluation of Safety and Efficiency of Metreleptin Treatment for Patients With Multiple Symmetric Lipomatosis (MSL)
PHASE2Active, not recruiting
4 participants
Started: Aug 1, 2023 · Completed: Oct 31, 2028
Locations (1)
Headquarters
London, UK
Map
Loading map...