450
Participants
Start Date
January 29, 2021
Primary Completion Date
February 20, 2026
Study Completion Date
March 19, 2027
Etavopivat Tablets Low dose
200 mg once daily
Etavopivat Tablets High dose
400 mg once daily
Placebo Tablets
Placebo once daily
Etavopivat Tablets
Selected dose once daily
[Legal] Alexandria Clinical Research LLC, Alexandria
Ain Shams University Hospital, Cairo
Ghana Institute of Clinical Genetics, Korle Bu Teaching Hospital (KBTH), Accra
Gertrude's Children's Hospital, Nairobi, Nairobi
Sultan Qaboos University Hospital, Muscat
Kintampo Health Research Centre (KHRC), Kintampo, Ghana, Kintampo
University of Abuja Teaching Hospital, Gwagwalada, Abuja, Abuja
American University of Beirut Medical center, Beirut
Baskent Universitesi Adana, Adana
Kombewa Clinical Research Centre, Kisumu
Aminu Kano Teaching Hospital (AKTH), Kano
Hacettepe Universitesi, Ankara
Columbia University Medical Center_New York, New York
Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche, Orbassano
Azienda Ospedaliera Universitaria San Luigi Gonzaga, Orbassano
Jacobi Medical Center, The Bronx
Children's Hospital at Montefiore, The Bronx
Montefiore Medical Center, The Bronx
Long Island Jewish Medical Center, New Hyde Park
Kings County Hospital, Brooklyn
NYC Health+Hospitals, Brooklyn
Al Kasr AL Aini Hospital, Cairo
Charité - Campus Virchow-Klinikum - Klinik für Pädiatrie mit Schwerpunkt Onkologie und Hämatologie, Berlin
The Children's Hospital of Philadelphia (CHOP), Philadelphia
Thomas Jefferson University Hospital, Philadelphia
Children's National Health Center, Washington D.C.
Children's National Health Hospital, Washington
[Legal] Alexandria Clinical Research LLC, Alexandria
Virginia Commonwealth University, Richmond
Virginia Commonwealth University, Richmond
General University Hospital of Patras, Rio
Centro per lo Studio e la Cura delle Amiloidosi Sistemiche Fondazione IRCCS Policlinico San Matteo, Pavia
Fondazione IRCCS Policlinico San Matteo, Pavia
Wake Forest Baptist Health, Winston-Salem
UNC School of Medicine, Chapel Hill
Duke University - Sickle Cell Center, Durham
Duke University Medical Center, Durham
East Carolina University (ECU) Physicians, Greenville
East Carolina University, Greenville
Hospital Universitario La Paz, Madrid
Universidad Autonoma de Madrid (UAM) - Hospital Universitario La Paz, Madrid
Levine Cancer Institute, Charlotte
Medical University of South Carolina, Charleston
Prisma Health-Upstate, Greenville
Emory University School of Medicine, Atlanta
Sonar Clinical Research, Atlanta
Emory University School of Medicine, Atlanta
Sonar Clinical Research, Atlanta
Children's Healthcare of Atlanta Investigational Medication Pharmacy, Atlanta
Augusta University Center for Blood Disorders., Augusta
Center for Blood Disorders Augusta University, Augusta
Arnold Palmer Children's Hospital, Orlando
Office of Gershwin T. Blyden, MD, Hollywood
Foundation for Sickle Cell Disease Research, Hollywood
Mersin University Medical Faculty Hospital, Hematology, Mersin
University Of Miami, Miami
VM Medical Park Mersin Hospital, Mersin
CHU Montpellier, Hôpital Saint-Eloi, Montpellier
Azienda Ospedale Universita Padova, Padua
Univ of Alabama Birmingham, Birmingham
University of Alabama at Birmingham (UAB), Birmingham
Methodist University Hospital, Memphis
St. Jude Children's Research Hospital (SJCRH), Memphis
KEMRI Kondele Children Hospital, Kisumu, Kisumu
KEMRI Siaya Clinical Research Annex Siaya County Referral Hospital, Siaya, Kisumu
General Hospital Of Larissa Koutlibaneio And Triantafylleio, Larissa
General University Hospital of Larissa, Larissa
Sydnawy University Hospital, Zagazig
Neuro-Behavioral Clinical Research, North Canton
Cincinnati Childrens Hospital Medical Center, Cincinnati
Hospital De Cruces, Barakaldo
Barbara Ann Karmanos Cancer Institute, Detroit
Detroit Medical Center (DMC) - Children's Hospital of Michigan (CHM), Detroit
Hospital Universitario de Cruces, Barakaldo
Blood Center of Wisconsin (BCW), Milwaukee
Versiti Blood Center of Wisconsin, Milwaukee
'Ippokrateio' General Hospital of Thessaloniki, Thessaloniki
"General Hospital of Thessaloniki Hippokration", Thessaloniki
University of Illinois at Chicago, Chicago
Washington University School of Medicine_St. Louis, St Louis
Hôpital Emile Muller, Mulhouse
Uniklinik Heidelberg - Klinik für Pädiatrische Onkologie, Hämatologie, Immunologie und Pneumologie, Heidelberg
University Hospital of Heidelberg, Heidelberg
Hospices Civils de Lyon-Hopital Edouard Herriot, Lyon
Hôpital Edouard HERRIOT, Lyon
Children's Hosp-New Orleans, New Orleans
Children's Hospital New Orleans, New Orleans
Woodland International Research Group, Little Rock
Ap-Hp-Hopital Robert Debre, Paris
[Legal] Baylor College of Medicine, Houston
Baylor College of Medicine, Houston
The University of Texas Health Science Center at Houston, Houston
UT Health University of Texas, Houston
Universitätsklinikum Freiburg-Zentrum für Kinder- und Jugendmedizin, Freiburg im Breisgau
Prince Mohammad Bin Naser Hospital, Jizan
Phoenix Children's Hsptl, Phoenix
Collaborative Neuroscience Research, LLC., Long Beach
University of California, Irvine, Irvine
University Of California Irvine, Orange
Ap-Hp-Hopital Henri Mondor, Créteil
Hôpital Henri Mondor, Créteil
Mary Bridge Children's Health, Tacoma
Lagos University Teaching Hospital, Lagos, Lagos
University of Nigeria Teaching Hospital, Enugu, Lagos
Cairo University, Cairo
K.J Somaiya Hospital and Research Centre, Mumbai
Victoria Hospital, Bangalore, Bangalore
Barau Dikko Teaching Hospital, Kaduna, Kaduna
University of Connecticut, Farmington
Yale University, New Haven
Boston Medical Center, Boston
University of Nebraska Medical Center, Omaha
Queens Hospital Center, Jamaica
Providence Hematolgy, Vancouver
The Hospital for Sick Children, Toronto
University Health Network - Toronto General Hospital, Toronto
Universite de Montreal - Centre Hospitalier Universitaire (CHU) Sainte-Justine, Montreal
Providence Hematology, Vancouver
Alexandria Clinical Research Center, Alexandria
Alexandria Faculty of Medicine - Clinical Research Center, Alexandria
CHU Paris - Hôpital Robert Debré, Paris
Univertatsklinikum Frankfurt, Frankfurt
UKE Hamburg, Hamburg
IRCCS Ospedale Pediatrico Bambino Gesu, Rome
Nini Hospital, Tripoli
General University Hospital of Patras, Pátrai
Gen Hosp Athens Ippokrateio,B' Uni Clinic Internal Medicine, Athens
Hippocratio General Hospital, Athens
Hospital Nini, Tripoli
King Khaled University Hospital,King Saud Univ. Med. City, Riyadh
Hospital Universitari Vall d'Hebron de Barcelona, Barcelona
Hospital Vall d'Hebron, Barcelona
Guys and St Thomas NHS Foundation Trust / Evelina Childrens Hospital, London
Kings College Hospital, London
Hammersmith Hospital - Imperial College Healthcare NHS Trust, London
Imperial College Healthcare NHS Trust - Hammersmith Hospital, London
Churchill Hospital, Oxford
Oxford University Hospitals NHS Trust - Churchill Hospital - Cancer and Haematology Centre, Oxford
The Royal Hallamshire Hospital, Sheffield Teaching Hospital NHS Foundation Trust, Sheffield
Royal Hallamshire Hospital, Sheffield
Lead Sponsor
Collaborators (1)
Novo Nordisk A/S
INDUSTRY
Forma Therapeutics, Inc.
INDUSTRY