Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database

RecruitingOBSERVATIONAL
Enrollment

500

Participants

Timeline

Start Date

April 8, 2020

Primary Completion Date

April 8, 2050

Study Completion Date

April 8, 2050

Conditions
Neuronal Ceroid LipofuscinosisBatten DiseaseCLN1 DiseaseCLN2 DiseaseCLN3 DiseaseCLN4 DiseaseCLN5 DiseaseCLN6 DiseaseCLN7 DiseaseCLN8 DiseaseCLN10 DiseaseCLN11 DiseaseCLN12 DiseaseCLN13 DiseaseCLN14 Disease
Interventions
OTHER

Natural History

Natural History and Clinical Follow Up.

Trial Locations (1)

20246

RECRUITING

University Medical Center Hamburg-Eppendorf, Hamburg

All Listed Sponsors
lead

Universitätsklinikum Hamburg-Eppendorf

OTHER