213
Participants
Start Date
May 21, 2021
Primary Completion Date
September 12, 2023
Study Completion Date
October 5, 2023
Mavodelpar
Once daily
Placebo
Once daily
University of Auckland, Auckland
Semmelweis University Insitute of Genomics and Rare Disorders, Budapest
Royal North Shore Hospital, St Leonards
Rigshospitalet, University of Copenhagen, Copenhagen
The Alfred Hospital, Melbourne
PARC Clinical Research, Adelaide
University of Pécs Clinical Centre, Department of Neurology, Pécs
Hospital Clinic de Barcelona, Barcelona
Columbia University Irving Medical Center, New York
General University Hospital in Prague, Prague
UPMC Children's Hospital of Pittsburgh, Pittsburgh
The Children's Hospital of Philadelphia, Philadelphia
"Fondazione IRCCS Istituto Neurologico Carlo Besta UOC Genetica Medica e Neurogenetica", Milan
Myology Institute, University of Florida, Gainesville
IRCCS Istituto delle Scienze Neurologiche, Bologna
Akron Children's Hospital, Akron
Hospital Universitari i Politècnic La Fe, Valencia
Centre Hospitalier Universitaire d' Angers, Angers
University Hospital Bonn Clinic and Polyclinic for Neurology, Bonn
Azienda Ospedaliero-Universitaria Pisana Dipartimento di specialita' mediche UOC Neurologia, Pisa
Hôpital Roger Salengro, Lille
Hôpitaux Universitaires de Strasbourg, Strasbourg
Hôpital Neurologique Pierre Wertheimer, Bron
University of Texas SouthWestern Medical Center, Dallas
Hôpital Pitié-Salpêtrière, Paris
Centre for the Treatment of Pediatric Neurodegenerative Disease, University of Texas McGovern Medical School, Houston
Medical Center of the University of Munich Friedrich Baur Institute at the Neurological Clinic and Polyclinic, Munich
University of California, San Diego, La Jolla
A.O.U Policlinico di Messina U.O.C Neurologia e Malattie Neuromuscolari, Messina
Massachusetts General Hospital, Boston
University Hospital Leuven, Leuven
M.A.G.I.C. Clinic (Metabolics and Genetics in Calgary), Calgary
Adult Metabolic Diseases Clinic, Vancouver General Hospital, Vancouver
CHU de Nice, Nice
Fondazione Policlinico Universitario Agostino Gemelli IRCCS Neurophysiopathology Unit, Rome
Radboud Universitair Medisch Centrum, Nijmegen
Haukeland University Hospital, Bergen
Hospital Universitario 12 de Octubre, Madrid
Queen Square Centre for Neuromuscular Diseases, London
Salford Royal NHS Foundation Trust, Salford
The Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Reneo Pharma Ltd
INDUSTRY