A Study of Ponatinib With Chemotherapy in Children, Teenagers, and Adults With Philadelphia Chromosome-Positive Acute Lymphoblastic Leukemia

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

11

Participants

Timeline

Start Date

February 24, 2021

Primary Completion Date

December 19, 2023

Study Completion Date

July 19, 2024

Conditions
Pediatric Philadelphia Chromosome-positive Acute Lymphoblastic Leukemia (Ph+ALL)Ph+ Mixed Phenotype Acute Leukemia (MPAL)Philadelphia Chromosome-Like ALL (Ph-like ALL)
Interventions
DRUG

Ponatinib

Ponatinib tablets.

DRUG

Chemotherapy Agents

Chemotherapy agents for reinduction include vincristine, dexamethasone, polyethylene glycol (PEG)-asparaginase (Erwinia asparaginase when PEG-asparaginase is not available), daunorubicin. Agents for intrathecal (IT) chemotherapy, central nervous system (CNS)-1/2: IT methotrexate chemotherapy, or CNS-3: triple intrathecal (ITT) methotrexate, hydrocortisone, cytarabine. Chemotherapy agents for consolidation include dexamethasone, vincristine, methotrexate, PEG-asparaginase (Erwinia asparaginase when PEG-asparaginase is not available), cyclophosphamide, etoposide, CNS-1/2: IT methotrexate chemotherapy, CNS-3: ITT chemotherapy methotrexate, hydrocortisone, cytarabine. The doses for chemotherapy agents for reinduction will be given as per standard of care.

Trial Locations (64)

165

IRCCS Ospedale Pediatrico Bambino Gesu - INCIPIT - PIN, Rome

3052

Royal Children's Hospital Melbourne - PIN, Parkville

3080

Seoul National University Hospital, Seoul

3722

Severance Hospital Yonsei University Health System, Seoul

4101

Queensland Childrens Hospital, South Brisbane

4530

Instituto Nacional de Pediatria, Mexico City

5505

Asan Medical Center - PPDS, Seoul

6009

Perth Childrens Hospital, Nedlands

6591

The Catholic University of Korea, Seoul St. Mary's Hospital, Seoul

8035

Hospital Universitario Vall d'Hebron - PPDS, Barcelona

10126

Ospedale Infantile Regina Margherita - INCIPIT - PIN, Turin

13385

Assistance Publique Hopitaux de Marseille, Marseille

15006

Fakultni nemocnice v Motole, Prague

16147

Istituto G Gaslini Ospedale Pediatrico IRCCS - INCIPIT - PIN, Genoa

19104

Children's Hospital of Philadelphia, Philadelphia

19803

Alfred I Dupont Hospital For Children, Wilmington

20900

Fndazione MBBM (MONZA E BRIANZA PER IL BAMBINO E LA SUA MAMMA) - c/o Centro Maria Letizia Verga, Monza

28009

Hospital Infantil Universitario Nino Jesus - PIN, Madrid

31059

Hopital Des Enfants, Toulouse

35200

Hopital Sud, Rennes

38105

St Jude Children's Research Hospital, Memphis

41013

Hospital Universitario Virgen del Rocio - PPDS, Seville

43205

Nationwide Children's Hospital, Columbus

44340

Nuevo Hospital Civil de Guadalajara Dr. Juan I. Menchaca, Guadalajara

45229

Cincinnati Children's Hospital Medical Center - PIN, Cincinnati

60611

Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago

61300

Fakultni nemocnice Brno, Brno

64108

Children's Mercy Hospital and Clinica, Kansas City

64460

Hospital Universitario Dr. Jose Eleuterio Gonzalez, Monterrey

72202

Arkansas Children's Hospital, Little Rock

75019

Hopital Robert Debre, Paris

90027

Children's Hospital Los Angeles, Los Angeles

92123

Rady Childrens Hospital San Diego - PIN, San Diego

200040

Children's Hospital of Shanghai, Shanghai

200127

Shanghai Childrens Medical Center, Shanghai

215025

Children's Hospital of Soochow University, Suzhou

230601

The Second Hospital of Anhui Medical University, Hefei

250012

Qilu Hospital of Shandong University, Jinan

300020

Institute of Hematology and Blood Diseases Hospital Chinese Academy of Medical Sciences, Tianjin

400014

Children's Hospital of Chongqing Medical University, Chongqing

430022

Union Hospital Tongji Medical College Huazhong University of Science and Technology, Wuhan

430030

Tongji Hospital Tongji Medical College Huazhong University of Science and Technology, Wuhan

550004

The Affiliated Hospital of Guizhou Medical University, Guiyang

610041

West China Second University Hospital, Sichuan Univesity, Chengdu

94143-3010

UCSF Medical Comprehensive Cancer, San Francisco

46202-5128

Riley Hospital For Children, Indianapolis

75235-9063

Childrens Medical Center Research Institute at UT Southwestern, Dallas

B1629AHJ

Hospital Universitario Austral, Pilar

C1199ABB

Hospital Italiano de Buenos Aires, Buenos Aires

81520-060

Rua Ramiro Barcelos, 2350, Curitiba

90020-090

Irmandade Da Santa Casa de Misericordia de Porto Alegre, Porto Alegre

90035-903

Hospital de Clinicas de Porto Alegre (HCPA) - PPDS, Porto Alegre

14784-400

Fundacao Pio XII Hospital de Cancer de Barretos, Barretos

14051-140

Hospital Das Clinicas da Faculdade de Medicina de Ribeirao Preto - USP, Ribeirão Preto

04039-001

Graacc Grupo de Apoio Ao Adolescente E A Crianca Com Cancer, São Paulo

08270-070

Hospital Santa Marcelina, São Paulo

3584 CS

Princess Maxima Center for Pediatric Oncology - PIN, Utrecht

30-663

Uniwersytecki Szpital Dzieciecy, Krakow

41-800

SPSK Nr 1 im. Prof.Stanislawa Szyszko Slaskiego Uniwersytetu Medycznego, Zabrze

1099-023

Instituto Portugues de Oncologia de Lisboa Francisco Gentil, E.P.E., Lisbon

4200-072

Instituto Portugues de Oncologia Do Porto Francisco Gentil Epe - PPDS, Porto

SM2 5PT

Royal Marsden Hospital - Surrey, Surrey Quays

CB2 0QQ

Cambridge University Hospitals NHS Foundation Trust, Cambridge

G3 8SJ

Royal Hospital for Children (Glasgow) - PPDS - PIN, Glasgow

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Takeda

INDUSTRY