A Study to Assess the Safety, Tolerability, and Effect on Disease Progression of BIIB105 in Participants With Amyotrophic Lateral Sclerosis (ALS) and Participants With the ALS Ataxin-2 (ATXN2) Genetic Mutation

PHASE1/PHASE2TerminatedINTERVENTIONAL
Enrollment

99

Participants

Timeline

Start Date

September 28, 2020

Primary Completion Date

August 13, 2024

Study Completion Date

August 13, 2024

Conditions
Amyotrophic Lateral Sclerosis
Interventions
DRUG

BIIB105

Administered as specified in the treatment arm.

DRUG

Placebo

Administered as specified in the treatment arm.

Trial Locations (17)

19104

University of Pennsylvania, Philadelphia

21218

ALS Clinic - Department of Neurology, Neuromuscular Division, Johns Hopkins University, School of Medicine, Baltimore

30322

The Emory Clinic, Atlanta

32224

Mayo Clinic Florida, Jacksonville

32806

Orlando Health, Orlando

63110

Washington University, School of Medicine, St Louis

77030

Houston Methodist Neurological Institute, Houston

80045

University of Colorado Hospital - Neuroscience Center -Anschutz Medical Campus, Aurora

84132

University of Utah, Salt Lake City

85013

Barrow Neurological Institute, Phoenix

92037

University of California San Diego Medical Center, La Jolla

94305

Stanford Neuromuscular Research Center, Palo Alto

20007-2113

Georgetown University, Washington D.C.

02114

Massachusetts General Hospital, Boston

H3A 2B4

Montreal Neurological Institute-Hospital, Montreal

Unknown

A.O.U. Città della salute e della scienza di Torino, Torino

3584 CX

UMC Utrecht, Utrecht

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Biogen

INDUSTRY