46
Participants
Start Date
January 4, 2021
Primary Completion Date
October 9, 2025
Study Completion Date
October 9, 2025
Nusinersen
Administered as specified in the treatment arm.
Children's Hospital Philadelphia - Neurology, Philadelphia
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan
Universitaetsklinikum Hamburg-Eppendorf, Hamburg
Children's Hospital of The King's Daughters, Norfolk
Hospital Universitario La paz, Madrid
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Arkansas Children's Hospital Research Institute, Little Rock
Children's Hospital Colorado, Aurora
University of Utah, Salt Lake City
Stanford Neuromuscular Research, Palo Alto
Oregon Health and Science University (OHSU), Portland
Schneider Children's Medical Center, Petah Tikva
Massachusetts General Hospital, Boston
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma
Hospital Sant Joan de Déu, Esplugues Del Llobregat
Lead Sponsor
Biogen
INDUSTRY