241
Participants
Start Date
April 22, 2021
Primary Completion Date
April 30, 2030
Study Completion Date
April 30, 2030
RECRUITING
Hôpital Universitaire des Enfants Reine Fabiola, Brussels
RECRUITING
UZ Leuven, Leuven
RECRUITING
University Hospital Gent, Ghent
RECRUITING
Istituto Giannina Gaslini, Genoa
RECRUITING
Karolinska Universitetssjukhuset Solna, Stockholm
RECRUITING
The Children's Hospital of Philadelphia, Philadelphia
RECRUITING
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
RECRUITING
Children's Hospital of the King's Daughters, Norfolk
RECRUITING
Azienda Ospedale Università Padova, Padua
RECRUITING
Zentrum für Kinderheilkunde und Jugendmedizin Uniklinikum Giessen Marburg (UKGM), Standort Giessen, Giessen
RECRUITING
Nationwide Children's Hospital, Columbus
RECRUITING
Anne & Robert H. Lurie Children's Hospital of Chicago, Chicago
RECRUITING
Arkansas Children's, Little Rock
RECRUITING
University of Texas Southwestern Medical Center, Dallas
COMPLETED
University of Utah Hospital, Salt Lake City
COMPLETED
Barrow Neurological Institute, Phoenix
RECRUITING
University of California San Diego, La Jolla
RECRUITING
University of California, Davis Health Dept of PM&R, Sacramento
COMPLETED
Oregon Health and Science University, Portland
RECRUITING
Hospital de Clinicas de Porto Alegre (HCPA) - PPDS, Porto Alegre
COMPLETED
Children's Hospital - London Health Science Centre, London
RECRUITING
Universitätsklinikum Essen, Essen
RECRUITING
Hospital Sant Joan de Déu Universidad de Barcelona, Barcelona
RECRUITING
Lokman Hekim Etlik Hastanesi, Ankara
RECRUITING
UCL Institute of Child Health & Great Ormond Street Hospital for Children, London
RECRUITING
Institute of Genetic Medicine, International Centre for Life, Newcastle upon Tyne
Sarepta Therapeutics, Inc.
INDUSTRY