A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

RecruitingOBSERVATIONAL
Enrollment

241

Participants

Timeline

Start Date

April 22, 2021

Primary Completion Date

April 30, 2030

Study Completion Date

April 30, 2030

Conditions
Limb-girdle Muscular Dystrophy
Trial Locations (26)

1020

RECRUITING

Hôpital Universitaire des Enfants Reine Fabiola, Brussels

3000

RECRUITING

UZ Leuven, Leuven

9000

RECRUITING

University Hospital Gent, Ghent

16147

RECRUITING

Istituto Giannina Gaslini, Genoa

17176

RECRUITING

Karolinska Universitetssjukhuset Solna, Stockholm

19104

RECRUITING

The Children's Hospital of Philadelphia, Philadelphia

20122

RECRUITING

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan

23507

RECRUITING

Children's Hospital of the King's Daughters, Norfolk

35129

RECRUITING

Azienda Ospedale Università Padova, Padua

35392

RECRUITING

Zentrum für Kinderheilkunde und Jugendmedizin Uniklinikum Giessen Marburg (UKGM), Standort Giessen, Giessen

43205

RECRUITING

Nationwide Children's Hospital, Columbus

60611

RECRUITING

Anne & Robert H. Lurie Children's Hospital of Chicago, Chicago

72202

RECRUITING

Arkansas Children's, Little Rock

75201

RECRUITING

University of Texas Southwestern Medical Center, Dallas

84112

COMPLETED

University of Utah Hospital, Salt Lake City

85013

COMPLETED

Barrow Neurological Institute, Phoenix

92037

RECRUITING

University of California San Diego, La Jolla

95817

RECRUITING

University of California, Davis Health Dept of PM&R, Sacramento

97068

COMPLETED

Oregon Health and Science University, Portland

90035-903

RECRUITING

Hospital de Clinicas de Porto Alegre (HCPA) - PPDS, Porto Alegre

N6C 2R5

COMPLETED

Children's Hospital - London Health Science Centre, London

D-45147

RECRUITING

Universitätsklinikum Essen, Essen

08950

RECRUITING

Hospital Sant Joan de Déu Universidad de Barcelona, Barcelona

06100

RECRUITING

Lokman Hekim Etlik Hastanesi, Ankara

WC1N 1EH

RECRUITING

UCL Institute of Child Health & Great Ormond Street Hospital for Children, London

NE1 3BZ

RECRUITING

Institute of Genetic Medicine, International Centre for Life, Newcastle upon Tyne

All Listed Sponsors
lead

Sarepta Therapeutics, Inc.

INDUSTRY