Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

77

Participants

Timeline

Start Date

August 18, 2020

Primary Completion Date

June 17, 2024

Study Completion Date

October 25, 2028

Conditions
Hemophilia A
Interventions
BIOLOGICAL

PF-07055480 (giroctocogene fitelparovec): Recombinant AAV2/6 Human Factor VIII Gene Therapy

Single IV infusion

Trial Locations (36)

3004

The Alfred Hospital, Melbourne

10002

National Taiwan University Hospital, Taipei

10249

Vivantes Klinikum im Friedrichshain, Berlin

11527

"General Hospital of Athens Hippokration", Athens

27310

Gaziantep University Sahinbey Research and Training Hospital, Gaziantep

35100

Ege University Medical Faculty, Pediatric Hematology, Izmir

Ege University Medical Faculty, Izmir

47012

H.U. Rio Hortega, Valladolid

50134

Azienda Ospedaliero Universitaria Careggi SODc Malattie Emorragiche e della Coagulazione, Florence

60590

Klinikum der Johann Wolfgang Goethe-Universitaet, Medizinische Klinik II, Frankfurt am Main

75015

Hopital Necker, Paris

80131

Dip. di Medicina Clinica e Chirurgia, Università degli Studi di Napoli Federico II - UOC di Medicina, Napoli

94040

NOW Physical Therapy, Mountain View

94063

Imaging Clinic at Stanford Medicine Outpatient Center in Redwood City, Redwood City

94143

UCSF IDS Pharmacy, San Francisco

University of California, San Francisco - Clinical Research Center, San Francisco

University of California, San Francisco - Moffitt/Long Inpatient Hematology, San Francisco

University of California, San Francisco - Outpatient Hematology Clinic, San Francisco

94304

Clinical and Translational Research Unit (CTRU), Palo Alto

Lucile Packard Childrens Hospital, Palo Alto

94305

Stanford Health Care, Stanford

98101

Washington Institute for Coagulation, Seattle

98195

University of Washington Medical Center - Translational Research Unit (TRU), Seattle

13083-878

Centro de Hematologia e Hemoterapia de Campinas - Hemocentro UNICAMP, Campinas

L8N 3Z5

McMaster University Medical Centre - Hamilton Health Sciences, Hamilton

L8V 1C3

Juravinski Hospital - Hamilton Health Sciences, Hamilton

115 27

General Hospital of Athens ''Laiko'', Athens

00161

"Università degli studi di Roma La Sapienza- Policlinico Umberto I", Roma

466-8560

Nagoya University Hospital - Transfusion Medicine, Nagoya

350-0495

Saitama Medical University Hospital, Iruma-gun

Unknown

King Faisal Specialist Hospital & Research Center, Riyadh

05278

Kyung Hee University Hospital at Gangdong, Seoul

08035

Hospital Universitari Vall d'Hebron, Barcelona

205 02

Skåne University Hospital, Malmo

01130

Adana Acibadem Hospital, Adana

SE1 7EH

Guy's and St. Thomas' NHS Foundation Trust, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Pfizer

INDUSTRY