Response to CFTR Modulators in CF Patients Under 18 Years

RecruitingOBSERVATIONAL
Enrollment

600

Participants

Timeline

Start Date

January 1, 2020

Primary Completion Date

July 1, 2025

Study Completion Date

January 1, 2026

Conditions
Cystic Fibrosis in Children
Interventions
DRUG

CFTR Modulators

CFTR modulators as recommended in routine care by the french health authorities

Trial Locations (1)

75015

RECRUITING

Sermet-Gaudelus Isabelle, Paris

All Listed Sponsors
lead

Societe Francaise de la Mucoviscidose

OTHER