154
Participants
Start Date
January 29, 2020
Primary Completion Date
August 19, 2022
Study Completion Date
August 19, 2022
Trofinetide
Trofinetide solution of 30-60 mL based on subject's weight at Baseline, administered twice daily by mouth or gastrostomy tube (G-tube)
Montefiore Medical Center, Children's Hospital at Montefiore, The Bronx
Children's Hospital of Philadelphia, Philadelphia
Kennedy Krieger Institute - Clinical Trials Unit, Baltimore
The University of North Carolina at Chapel Hill, Chapel Hill
Greenwood Genetic Center, Greenwood
Emory Genetics Clinical Trial Center, Atlanta
Children Medical Services, Tampa
University of Alabama at Birmingham, Birmingham
Vanderbilt University Medical Center, Nashville
Cleveland Clinic, Cleveland
Cincinnati Children's Hospital Medical Center, Cincinnati
Gillette Children's Specialty Healthcare, Saint Paul
Rush University Medical Center, Chicago
Washington University School of Medicine, St. Louis Children's Hospital, St Louis
Texas Children's Hospital, Houston
Children's Hospital Colorado, Aurora
Translational Genomics Research Institute (TGen), Phoenix
University of California, San Diego, La Jolla
UC Davis MIND Institute, Sacramento
Seattle Children's, Seattle
Boston Children's Hospital, Boston
Lead Sponsor
ACADIA Pharmaceuticals Inc.
INDUSTRY