31
Participants
Start Date
July 31, 2020
Primary Completion Date
July 1, 2022
Study Completion Date
July 1, 2026
Cysteamine Bitartrate
ERT
UZA, Antwerp
HUDERF, Brussels
UCL Saint-Luc, Brussels
UZ Gent, Ghent
UZ Leuven, Leuven
CHC, Liège
CHU, Liège
Lead Sponsor
Chiesi SA/NV
OTHER