French Register of Patients With Spinal Muscular Atrophy

RecruitingOBSERVATIONAL
Enrollment

1,000

Participants

Timeline

Start Date

January 31, 2020

Primary Completion Date

January 31, 2029

Study Completion Date

January 31, 2029

Conditions
Spinal Muscular Atrophy
Trial Locations (1)

92380

RECRUITING

Unité neuromusculaire, Service de Neurologie et Réanimation Pédiatrique, (French neuromuscular reference network (FILNEMUS), Hôpital Raymond Poincaré,, Garches

All Listed Sponsors
lead

Assistance Publique - Hôpitaux de Paris

OTHER