95
Participants
Start Date
January 15, 2019
Primary Completion Date
December 30, 2024
Study Completion Date
July 30, 2029
Carglumic Acid
Maintenance therapy with carglumic acid
RECRUITING
Hopital de la Conception, Marseille
RECRUITING
Hôpital de la Timone, Marseille
RECRUITING
San Paola Hospital, ASST Santi Paolo e Carlo, Milan
RECRUITING
Azienda Ospedaliera San Gerardo Monza, Monza
RECRUITING
Hospital Infantil Universitario Nino Jesus, Madrid
RECRUITING
Hospital 12 de Octubre, Madrid
RECRUITING
Hospital Universitario La Paz, Madrid
RECRUITING
Klinikum Bremen Mitte, Prof. Hess Kinderklinik, Bremen
RECRUITING
Hospital Universitario Virgen de la Arrixaca, Murcia
RECRUITING
Hopital Des Enfants, CHU de Bordeaux-GH Pellegrin, Bordeaux
RECRUITING
Hospital Universitario Virgen del Rocio, Seville
RECRUITING
Azienda Ospedaliero Universitaria Meyer, Florence
RECRUITING
CHU de Nancy - Hopitaux de Brabois, Nancy
RECRUITING
Nouvel Hopital Civil, Strasbourg
RECRUITING
Hopital de Hautepierre, Strasbourg
RECRUITING
Hôpital Necker Enfants Malades, Paris
RECRUITING
CHU de Rouen, Rouen
RECRUITING
Azienda Ospedaliera Universitaria Federico II, Napoli
RECRUITING
Milan Policlinico University, Milan
RECRUITING
University Hospital of Padova, Padua
RECRUITING
Turin University Hospital, Turin
RECRUITING
AMM hospital val d'hebron, Barcelona
RECRUITING
Sant Joan de Deu, Barcelona
RECRUITING
Universitario de Cruces, Bilbao
RECRUITING
Universitario Ramon y Cajal Madrid, Madrid
RECRUITING
Universitario Miguel Servet, Zaragoza
TERMINATED
NÄL, Trollhättan
RECRUITING
Oslo University Hospital, Oslo
RECRUITING
Hospital Universitario Son Espases, Palma de Mallorca
RECRUITING
Guy's and St. Thomas' Hospital NHS Foundation Trust, London
RECRUITING
Great Ormond Street Hospital, London
RECRUITING
Sheffield Children's Hospital NHS Foundation Trust, Sheffield
Recordati Rare Diseases
INDUSTRY