Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

RecruitingOBSERVATIONAL
Enrollment

700

Participants

Timeline

Start Date

September 25, 2018

Primary Completion Date

June 30, 2038

Study Completion Date

June 30, 2038

Conditions
Spinal Muscular Atrophy (SMA)
Interventions
OTHER

Prospective observational registry

This prospective observational registry will assess long-term outcomes of patients with a diagnosis of SMA.

DRUG

Zolgensma

Zolgensma will be given to patients as per normal clinical practice and clinical care will not be mandated by the protocol. As such, the decision to prescribe Zolgensma is separate from the decision to include the patient in this study

Trial Locations (99)

333

RECRUITING

Chang Gung Memorial Hospital Linkou Branch, Taoyuan District

11217

RECRUITING

Taipei Veterans General Hospital, Taipei

11794

RECRUITING

The State University of New York, Stony Brook

13620

RECRUITING

Seoul National University Bundang Hospital, Seongnam-si

14642

RECRUITING

University of Rochester Medical Center, Rochester

15224

RECRUITING

University of Pittsburgh Medical Center, Pittsburgh

16995

RECRUITING

Yongin Severance Hospital, Yongin-si

17033

RECRUITING

Penn State Hershey, Hershey

22908

RECRUITING

University of Virginia Health System, Charlottesville

23298

RECRUITING

Virginia Commonwealth University Health System, Richmond

23507

RECRUITING

Children's Hospital of The King's Daughters, Norfolk

27705

RECRUITING

Duke Health, Durham

29615

RECRUITING

Prisma Health, Greenville

32803

COMPLETED

Adventist Health System - Florida, Orlando

33155

COMPLETED

Nicklaus Children's Hospital, Miami

33157

RECRUITING

Jackson South Medical Center, Palmetto Bay

33908

RECRUITING

Golisano Children's Hospital of Southwest Florida, Fort Myers

38103

RECRUITING

Methodist Le Bonheur Healthcare, Memphis

40202

RECRUITING

University of Louisville, Louisville

41944

RECRUITING

Kyungpook National University Hospital, Daegu

43205

RECRUITING

Nationwide Children's Hospital, Columbus

44106

COMPLETED

University Hospitals, Cleveland

46202

RECRUITING

Indiana University Health University Hospital (IUHUH), Indianapolis

50612

RECRUITING

Pusan National University Yangsan Hospital, Yangsan

53226

RECRUITING

Children's Hospital of Wisconsin, Milwaukee

53792

RECRUITING

University of Wisconsin, Madison

55455

RECRUITING

University of Minnesota, Minneapolis

63110

RECRUITING

Washington University School of Medicine in St. Louis, St Louis

65212

RECRUITING

University of Missouri Health System, Columbia

66160

RECRUITING

University of Kansas Medical Center, Kansas City

72202

RECRUITING

Arkansas Children's Hospital, Little Rock

73104

COMPLETED

Oklahoma University Medical Center, Oklahoma City

75207

COMPLETED

Children's Health, Dallas

76104

RECRUITING

Cook Children's, Fort Worth

77030

RECRUITING

Texas Children's Hospital, Houston

78207

RECRUITING

CHRISTUS Health, San Antonio

78731

COMPLETED

Child Neurology Consultants of Austin, Austin

80045

RECRUITING

Children's Hospital Colorado, Aurora

80756

RECRUITING

Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City

84113

RECRUITING

University of Utah, Salt Lake City

85016

RECRUITING

Phoenix Children's Hospital, Phoenix

85025

RECRUITING

Soroka Medical Centre, Beersheba

90027

RECRUITING

Children's Hospital of Los Angeles, Los Angeles

90095

RECRUITING

University of California Los Angeles Health, Los Angeles

92123

RECRUITING

Rady Children's Hospital San Diego, San Diego

92350

COMPLETED

Loma Linda University Health, Loma Linda

93636

RECRUITING

Valley Children's Healthcare, Madera

93638

RECRUITING

Children's Hospital of Orange County, Madera

95817

RECRUITING

University of California Davis Health System, Sacramento

98105

RECRUITING

Seattle Children's, Seattle

98405

RECRUITING

MultiCare Health System, Tacoma

100229

RECRUITING

National Taiwan University Hospital, Taipei

197341

RECRUITING

Almazov National Medical Research Centre, Saint Petersburg

404327

RECRUITING

China Medical University Hospital, Taichung

582201

RECRUITING

Tel-Aviv Sourasky Medical Center, Holon

4920235

RECRUITING

Schneider- Children's Medical Center, Petah Tikva

5822012

RECRUITING

Wolfson Medical Center, Holon

06034

RECRUITING

Connecticut Children's Medical Center, Farmington

06510

RECRUITING

Yale-New Haven Health System, New Haven

52242-1009

RECRUITING

University of Iowa, Iowa City

07960

RECRUITING

Atlantic Health System, Morristown

44308-1062

COMPLETED

Akron Children's Hospital, Akron

45229-3026

RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

97239-3098

RECRUITING

Oregon Health and Science University, Portland

124 62

RECRUITING

University General Hospital Attikon, Chaïdári

152 36

RECRUITING

Penteli Children's Hospital, Pentéli

115 27

RECRUITING

St. Sophia Children's Hospital, Thessaloniki

546 42

RECRUITING

General Hospital of Thessaloniki Ippokrateio, Thessaloniki

1 D01 XD99

RECRUITING

Children's University Hospital-UCD School of Medicine Scoil an Leighis, Dublin

480-1195

ACTIVE_NOT_RECRUITING

Aichi Medical University Hospital, Nagakute-shi

470-1192

ACTIVE_NOT_RECRUITING

Fujita Health University Hospital, Toyoake-shi

266-0007

ACTIVE_NOT_RECRUITING

Chiba children's Hospital, Chiba

830-0011

ACTIVE_NOT_RECRUITING

Kurume University Hospital, Kurume-shi

500-8717

ACTIVE_NOT_RECRUITING

Gifu Prefectural General Medical Center, Gifu

060-8543

ACTIVE_NOT_RECRUITING

Sapporo Medical University Hospital, Sapporo

761-0793

ACTIVE_NOT_RECRUITING

Kagawa University Hospital, Kita-gun

232-8555

ACTIVE_NOT_RECRUITING

Kanagawa Children's Medical Center, Yokohama

860-8556

ACTIVE_NOT_RECRUITING

Kumamoto University Hospital, Kumamoto

989-3126

ACTIVE_NOT_RECRUITING

Miyagi Children's Hospital, Sendai

080-0024

ACTIVE_NOT_RECRUITING

Obihiro Kosei Hospital, Hokkaido

524-0022

ACTIVE_NOT_RECRUITING

Shiga Medical Center for Children, Moriyama-shi

431-3192

ACTIVE_NOT_RECRUITING

Hamamatsu University School of Medicine, University Hospital, Hamamatsu

329-0498

ACTIVE_NOT_RECRUITING

Jichi Medical University Hospital, Shimotsuke-shi

160-0023

ACTIVE_NOT_RECRUITING

Tokyo Medical University Hospital, Shinjuku-ku

162-8655

ACTIVE_NOT_RECRUITING

Center Hospital of the National Center for Global Health and Medicine, Shinjuku-ku

910-8526

ACTIVE_NOT_RECRUITING

Fukui Prefectural Hospital, Fukui

051-0005

ACTIVE_NOT_RECRUITING

Nikko Memorial Hospital, Hokkaido

343-0845

ACTIVE_NOT_RECRUITING

Dokkyo Medical University Saitama Medical Center, Saitama

20-093

RECRUITING

Uniwersytecki Szpital Dzieciec, Lublin

300-6020

RECRUITING

CHUC - Hospital Pediatrico, Coimbra

1169-045

RECRUITING

Centro Hospitalar Universitaria de Lisboa Central, EPE, Lisbon

1649-035

RECRUITING

Centro Hospitalar Universitario Lisboa Norte, EPE, Lisbon

4050-371

RECRUITING

Centro Hospitalar Universitario de Porto, EPE, Porto

4200-319

RECRUITING

Centro Hospitalar Universitario de Sao Joao, EPE, Porto

041408

RECRUITING

Centrul de Recuperare pentru Copii dr. Nicolae Robanescu, Bucharest

041914

RECRUITING

Spitalul Clinic de Psihiatrie, Bucharest

03080

RECRUITING

Seoul National University Children's Hospital, Seoul

03722

RECRUITING

Severance Hospital, Seoul

06351

RECRUITING

Samsung Medical Centre, Seoul

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY