700
Participants
Start Date
September 25, 2018
Primary Completion Date
June 30, 2038
Study Completion Date
June 30, 2038
Prospective observational registry
This prospective observational registry will assess long-term outcomes of patients with a diagnosis of SMA.
Zolgensma
Zolgensma will be given to patients as per normal clinical practice and clinical care will not be mandated by the protocol. As such, the decision to prescribe Zolgensma is separate from the decision to include the patient in this study
RECRUITING
Chang Gung Memorial Hospital Linkou Branch, Taoyuan District
RECRUITING
Taipei Veterans General Hospital, Taipei
RECRUITING
The State University of New York, Stony Brook
RECRUITING
Seoul National University Bundang Hospital, Seongnam-si
RECRUITING
University of Rochester Medical Center, Rochester
RECRUITING
University of Pittsburgh Medical Center, Pittsburgh
RECRUITING
Yongin Severance Hospital, Yongin-si
RECRUITING
Penn State Hershey, Hershey
RECRUITING
University of Virginia Health System, Charlottesville
RECRUITING
Virginia Commonwealth University Health System, Richmond
RECRUITING
Children's Hospital of The King's Daughters, Norfolk
RECRUITING
Duke Health, Durham
RECRUITING
Prisma Health, Greenville
COMPLETED
Adventist Health System - Florida, Orlando
COMPLETED
Nicklaus Children's Hospital, Miami
RECRUITING
Jackson South Medical Center, Palmetto Bay
RECRUITING
Golisano Children's Hospital of Southwest Florida, Fort Myers
RECRUITING
Methodist Le Bonheur Healthcare, Memphis
RECRUITING
University of Louisville, Louisville
RECRUITING
Kyungpook National University Hospital, Daegu
RECRUITING
Nationwide Children's Hospital, Columbus
COMPLETED
University Hospitals, Cleveland
RECRUITING
Indiana University Health University Hospital (IUHUH), Indianapolis
RECRUITING
Pusan National University Yangsan Hospital, Yangsan
RECRUITING
Children's Hospital of Wisconsin, Milwaukee
RECRUITING
University of Wisconsin, Madison
RECRUITING
University of Minnesota, Minneapolis
RECRUITING
Washington University School of Medicine in St. Louis, St Louis
RECRUITING
University of Missouri Health System, Columbia
RECRUITING
University of Kansas Medical Center, Kansas City
RECRUITING
Arkansas Children's Hospital, Little Rock
COMPLETED
Oklahoma University Medical Center, Oklahoma City
COMPLETED
Children's Health, Dallas
RECRUITING
Cook Children's, Fort Worth
RECRUITING
Texas Children's Hospital, Houston
RECRUITING
CHRISTUS Health, San Antonio
COMPLETED
Child Neurology Consultants of Austin, Austin
RECRUITING
Children's Hospital Colorado, Aurora
RECRUITING
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
RECRUITING
University of Utah, Salt Lake City
RECRUITING
Phoenix Children's Hospital, Phoenix
RECRUITING
Soroka Medical Centre, Beersheba
RECRUITING
Children's Hospital of Los Angeles, Los Angeles
RECRUITING
University of California Los Angeles Health, Los Angeles
RECRUITING
Rady Children's Hospital San Diego, San Diego
COMPLETED
Loma Linda University Health, Loma Linda
RECRUITING
Valley Children's Healthcare, Madera
RECRUITING
Children's Hospital of Orange County, Madera
RECRUITING
University of California Davis Health System, Sacramento
RECRUITING
Seattle Children's, Seattle
RECRUITING
MultiCare Health System, Tacoma
RECRUITING
National Taiwan University Hospital, Taipei
RECRUITING
Almazov National Medical Research Centre, Saint Petersburg
RECRUITING
China Medical University Hospital, Taichung
RECRUITING
Tel-Aviv Sourasky Medical Center, Holon
RECRUITING
Schneider- Children's Medical Center, Petah Tikva
RECRUITING
Wolfson Medical Center, Holon
RECRUITING
Connecticut Children's Medical Center, Farmington
RECRUITING
Yale-New Haven Health System, New Haven
RECRUITING
University of Iowa, Iowa City
RECRUITING
Atlantic Health System, Morristown
COMPLETED
Akron Children's Hospital, Akron
RECRUITING
Cincinnati Children's Hospital Medical Center, Cincinnati
RECRUITING
Oregon Health and Science University, Portland
RECRUITING
University General Hospital Attikon, Chaïdári
RECRUITING
Penteli Children's Hospital, Pentéli
RECRUITING
St. Sophia Children's Hospital, Thessaloniki
RECRUITING
General Hospital of Thessaloniki Ippokrateio, Thessaloniki
RECRUITING
Children's University Hospital-UCD School of Medicine Scoil an Leighis, Dublin
ACTIVE_NOT_RECRUITING
Aichi Medical University Hospital, Nagakute-shi
ACTIVE_NOT_RECRUITING
Fujita Health University Hospital, Toyoake-shi
ACTIVE_NOT_RECRUITING
Chiba children's Hospital, Chiba
ACTIVE_NOT_RECRUITING
Kurume University Hospital, Kurume-shi
ACTIVE_NOT_RECRUITING
Gifu Prefectural General Medical Center, Gifu
ACTIVE_NOT_RECRUITING
Sapporo Medical University Hospital, Sapporo
ACTIVE_NOT_RECRUITING
Kagawa University Hospital, Kita-gun
ACTIVE_NOT_RECRUITING
Kanagawa Children's Medical Center, Yokohama
ACTIVE_NOT_RECRUITING
Kumamoto University Hospital, Kumamoto
ACTIVE_NOT_RECRUITING
Miyagi Children's Hospital, Sendai
ACTIVE_NOT_RECRUITING
Obihiro Kosei Hospital, Hokkaido
ACTIVE_NOT_RECRUITING
Shiga Medical Center for Children, Moriyama-shi
ACTIVE_NOT_RECRUITING
Hamamatsu University School of Medicine, University Hospital, Hamamatsu
ACTIVE_NOT_RECRUITING
Jichi Medical University Hospital, Shimotsuke-shi
ACTIVE_NOT_RECRUITING
Tokyo Medical University Hospital, Shinjuku-ku
ACTIVE_NOT_RECRUITING
Center Hospital of the National Center for Global Health and Medicine, Shinjuku-ku
ACTIVE_NOT_RECRUITING
Fukui Prefectural Hospital, Fukui
ACTIVE_NOT_RECRUITING
Nikko Memorial Hospital, Hokkaido
ACTIVE_NOT_RECRUITING
Dokkyo Medical University Saitama Medical Center, Saitama
RECRUITING
Uniwersytecki Szpital Dzieciec, Lublin
RECRUITING
CHUC - Hospital Pediatrico, Coimbra
RECRUITING
Centro Hospitalar Universitaria de Lisboa Central, EPE, Lisbon
RECRUITING
Centro Hospitalar Universitario Lisboa Norte, EPE, Lisbon
RECRUITING
Centro Hospitalar Universitario de Porto, EPE, Porto
RECRUITING
Centro Hospitalar Universitario de Sao Joao, EPE, Porto
RECRUITING
Centrul de Recuperare pentru Copii dr. Nicolae Robanescu, Bucharest
RECRUITING
Spitalul Clinic de Psihiatrie, Bucharest
RECRUITING
Seoul National University Children's Hospital, Seoul
RECRUITING
Severance Hospital, Seoul
RECRUITING
Samsung Medical Centre, Seoul
Lead Sponsor
Novartis Pharmaceuticals
INDUSTRY