Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

77

Participants

Timeline

Start Date

April 15, 2021

Primary Completion Date

January 31, 2026

Study Completion Date

January 31, 2026

Conditions
Propionic Acidemia
Interventions
BIOLOGICAL

mRNA-3927

mRNA-3927 dispersion for IV infusion

Trial Locations (35)

8950

ACTIVE_NOT_RECRUITING

Hospital Sant Joan de Deu - PIN, Esplugues de Llobregat

10029

RECRUITING

Icahn School of Medicine at Mount Sinai - Clinical Research Unit, New York

11211

ACTIVE_NOT_RECRUITING

King Faisal Specialist Hospital & Research Center - Riyadh, Riyadh

11564

NOT_YET_RECRUITING

King Fahad Medical City, Riyadh

13005

ACTIVE_NOT_RECRUITING

CHU de Marseille - Hôpital de la Timone, Marseille

14611

NOT_YET_RECRUITING

King Abdullah Children's Specialist Hospital, Riyadh

19104

RECRUITING

Children's Hospital of Philadelphia (CHOP), Philadelphia

21287

COMPLETED

Johns Hopkins Hospital, Adult Outpatient Clinical Research Unit, Baltimore

27710

RECRUITING

Duke University Medical System (Duke Health), Durham

28041

RECRUITING

Hospital Universitario 12 de Octubre, Madrid

33155

NOT_YET_RECRUITING

Nicklaus Children's Hospital, Miami

41013

ACTIVE_NOT_RECRUITING

Hospital Universitario Virgen del Rocio - PPDS, Seville

45229

COMPLETED

Cincinnati Children's Hospital Medical Center, Cincinnati

48109

RECRUITING

University of Michigan Hospitals, Ann Arbor

48903

RECRUITING

Hospital Universitario Cruces, Barakaldo

75019

RECRUITING

Hôpital Necker - Enfants Malades, Paris

77030

RECRUITING

Texas Children's Hospital, Houston

90027

NOT_YET_RECRUITING

UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles

90095

RECRUITING

Ronald Reagan UCLA Medical Center, Los Angeles

94304

RECRUITING

Lucile Packard Children's Hospital Stanford, Stanford

33606-3603

NOT_YET_RECRUITING

University of South Florida - 12901 Bruce B Downs, Tampa

02115

COMPLETED

Boston Children's Hospital, Boston

45229-3026

RECRUITING

Ann and Robert H Lurie Childrens Hospital of Chicago, Cincinnati

44106-2624

ACTIVE_NOT_RECRUITING

University Hospitals Cleveland Medical Center - 11100 Euclid Ave, Cleveland

T6G 2R7

RECRUITING

Stollery Children's Hospital University of Alberta, Edmonton

M5G 1X8

RECRUITING

Hospital For Sick Children, Toronto

470-1192

RECRUITING

Fujita Health University Hospital, Toyoake-shi

980-8574

RECRUITING

Tohoku University Hospital, Sendai

113-8519

ACTIVE_NOT_RECRUITING

National Center for Child Health and Development, Tokyo

3015 GD

RECRUITING

Erasmus MC, Rotterdam

3584 CX

ACTIVE_NOT_RECRUITING

Universitair Medisch Centrum Utrecht - PPDS, Utrecht

B15 2TH

RECRUITING

University Hospital Birmingham NHS Foundation Trust, Birmingham

B4 6NH

COMPLETED

Birmingham Children's Hospital, Birmingham

WC1N 3JH

RECRUITING

Great Ormond Street Hospital for Children NHS Foundation Trust, London

M13 9WL

RECRUITING

Willink Biochemical Genetics Unit - PPDS, Manchester

All Listed Sponsors
lead

ModernaTX, Inc.

INDUSTRY