Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

PHASE2RecruitingINTERVENTIONAL
Enrollment

99

Participants

Timeline

Start Date

November 7, 2019

Primary Completion Date

July 2, 2027

Study Completion Date

June 11, 2035

Conditions
Beta-Thalassemia
Interventions
DRUG

ACE-536

Specified dose on specified days

Trial Locations (26)

0

WITHDRAWN

Local Institution - 700, Beirut

10043

RECRUITING

Azienda Ospedaliero Universitaria S. Luigi Gonzaga, Orbassano

10330

RECRUITING

Chulalongkorn University Faculty of Medicine - King Chulalongkorn Memorial Hospital, Bangkok

10400

RECRUITING

Ramathibodi Hospital, Mahidol University, Phyathai

10700

RECRUITING

Siriraj Hospital Mahidol University, Bangkok

16128

RECRUITING

Ente Ospedaliero Ospedali Galliera - Centro della Microcitemia e delle Anemie Congenite, Genoa

35100

COMPLETED

Local Institution - 401, Izmir

45147

RECRUITING

Universitätsklinikum Essen, Essen

80131

RECRUITING

AOU dell'Universita degli Studi della Campania Luigi Vanvitelli, Napoli

89081

RECRUITING

Universitatsklinikum Ulm, Ulm

90027

COMPLETED

Local Institution - 601, Los Angeles

201303

RECRUITING

Post Graduate Institute of Child Health, Noida

400022

RECRUITING

MCGM - Comprehensive Thalassemia Care, Pediatric Hematology-Oncology & BMT Centre, Borivali (E), Mumbai

440001

RECRUITING

Kingsway Hospitals, Nagpur

500052

RECRUITING

Kamala Hospital and Research Center, Hyderabad

510120

RECRUITING

Sun Yat-sen Memorial Hospital, Sun Yat-Sen University, Guangzhou

510515

RECRUITING

Nanfang Hospital, Southern Medical University, Guangzhou

518028

RECRUITING

Shenzhen Second People's Hospital, Shenzhen

530021

NOT_YET_RECRUITING

Local Institution - 904, Nanning

RECRUITING

The First Affiliated Hospital of Guangxi Medical University, Nanning

610041

RECRUITING

West China Hospital - Sichuan University, Chengdu

632004

RECRUITING

Christian Medical College & Hospital, Vellore

700094

WITHDRAWN

Local Institution - 803, Kolkata

10065-4870

RECRUITING

New York Presbyterian Hospital, New York

115 27

RECRUITING

"General Children's Hospital Agia Sophia", Athens

00165

RECRUITING

Ospedale Pediatrico Bambino Gesù IRCCS, Rome

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA

INDUSTRY

lead

Celgene

INDUSTRY