Safety, Tolerability, and Efficacy of Zilucoplan in Subjects With Generalized Myasthenia Gravis

PHASE3CompletedINTERVENTIONAL
Enrollment

174

Participants

Timeline

Start Date

September 17, 2019

Primary Completion Date

December 30, 2021

Study Completion Date

December 30, 2021

Conditions
Myasthenia Gravis, Generalized
Interventions
DRUG

zilucoplan (RA101495)

Daily subcutaneous (SC) injection

DRUG

Placebo

Daily subcutaneous (SC) injection

Trial Locations (77)

5021

Site 140: Haukeland University Hospital / Health Bergen, Bergen

10021

Site 23: Hospital for Special Surgery, New York

10029

Site 47: Mount Sinai Hospital, New York

11021

Site 123: Northwell Health Neuroscience Institute, Great Neck

15212

Site 40: Allegheny Neurological Associates, Pittsburgh

20037

Site 27: George Washington University, Washington D.C.

20123

Site 132: Università Cattolica del Sacro Cuore - Campus di Milano, Roma

20133

Site 126: Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan

22908

Site 164: University of Virginia Health System, Charlottesville

27599

Site 22: University of North Carolina, Chapel Hill

27710

Site 15: Duke University, Durham

29425

Site 128: Medical University of South Carolina, Charleston

30912

Site 135: Augusta University Medical Center, Augusta

33175

Site 182: Gelasio Baras Neurology, Miami

33612

Site 25: University of South Florida, Tampa

36604

Site 41: Diagnostic and Medical Clinic, Mobile

37075

Site 150: Universitätsmedizin Göttingen, Göttingen

38018

Site 185: Neurology Clinic Cordova, Cordova

43210

Site 38: Ohio State University, Columbus

44195

Site 122: Cleveland Clinic, Cleveland

46202

Site 156: Indiana University Health Neuroscience Center, Indianapolis

48013

Site 138: Hospital Universitario de Basurto, Bilbao

48202

Site 33: Detroit medical Center - University Health Center, Detroit

48824

Site 49: Michigan State University, East Lansing

53215

Site 45: Center for Neurological Disorders, Milwaukee

55455

Site 127: University of Minnesota, Minneapolis

65212

Site 134: Neurology and Sleep Disorders Clinic, Columbia

66160

Site 32: Kansas University Medical Center Research Institute, Kansas City

67091

Site 137: Les Hôpitaux Universitaires de Strasbourg, Strasbourg

72076

Site 129: Universitätsklinikum Tübingen, Tübingen

75013

Site 105: Pitié-Salpêtrière University Hospital, Paris

75390

Site 19: University of Texas Southwestern, Dallas

78756

Site 131: Austin Neuromuscular Center, Austin

84132

Site 39: University of Utah, Salt Lake City

85028

Site 116: Neuromuscular Clinic and Research Center, Phoenix

89145

Site 117: Las Vegas Clinic, Las Vegas

90033

Site 4: University of Southern California, Los Angeles

91101

Site 220: Investigator Site, Pasadena

92868

Site 31: University of California Irvine, Orange

94115

Site 160: Forbes Norris MDA/ALS Research and Treatment Center, San Francisco

96817

Site 176: Hawaii Pacific Neuroscience, Honolulu

98195

Site 154: University of Washington, Seattle

06510

Site 24: Yale University, New Haven

60026-1339

Site 188: North Shore Medical Group - Glenview, Glenview

02035

Site 221: Neurology Center of New England, Foxborough

N6A 5A5

Site 44: London Health Sciences Centre University Hospital, London

H3A 2B4

Site 11: Montreal Neurological Institute and Hospital (McGill University), Montreal

Unknown

Site 191: Centre Hosptitalier Universitaire d'Angers, Angers

Site 204: Centre Hospitalier Régional Universitaire de Lille, Lille

Site 179: Kagawa University Hospital - Collagen disease/Rheumatic int, Kita-gun

Site 193: Krakowska Akademia Neurologii - Centrum Neurologii Kliniczne, Krakow

Site 211: Specjalistyczne Gabinety Sp. z o.o., Krakow

Site 168: Hospital de la Santa Creu i Sant Pau, Barcelona

06000

Site 118: Hôpital Pasteur, Nice

286-8520

Site 169: International University of Health and Welfare Narita Hospital, Narita

260-8677

Site 151: Chiba University Hospital, Chiba

025-0075

Site 136: General Hanamaki Hospital, Iwata

852-8501

Site 146: Nagasaki University Hospital, Nagasaki

063-0005

Site 152: Hokkaido Medical Center, Sapporo

983-8520

Site 144: Sendai Medical Center, Sendai

153-8515

Site 153: Toho University Ohashi Medical Center, Tokyo

160-0023

Site 163: Tokyo Medical University Hospital, Tokyo

160-8582

Site 141: Keio University Hospital, Tokyo

565-0871

Site 165: Osaka University Hospital, Tokyo

0450

Site 143: Oslo Universitetssykehus, Oslo

61-853

Site 209: Niepubliczny Zakład Opieki Zdrowotnej NEURO - KARD, Poznan

31-202

Site 192: Krakowski Szpital Specjalistyczny im. Jana Pawła II, Krakow

20-093

Site 205: Prywatny Gabinet Lekarski Urszula Chyrchel-Paszkiewicz, Lublin

Site 210: Clinhouse Centrum Medyczne, Lublin

67-100

Site 194: Twoja Przychodnia - Centrum Medyczne Nowa Sól, Nowa Sól

90-644

Site 214: AmiCare Centrum Medyczne, Lodz

01-868

Site 201: Centrum Medyczne Pratia - Warszawa, Warsaw

40-123

Site 195: Wielospecjalistyczna Poradnia Lekarska Synapsis, Katowice

40-650

Site 213: Niepubliczny Zakład Opieki Zdrowotnej NOVO-MED, Katowice

08035

Site 133: Hospital Universitari Vall d'Hebrón, Barcelona

OX3 9DU

Site 119: Oxford University Hospitals NHS Foundation Trust, Oxford

S10 2JF

Site 130: Royal Hallamshire Hospital, Sheffield

All Listed Sponsors
lead

Ra Pharmaceuticals, Inc.

INDUSTRY

NCT04115293 - Safety, Tolerability, and Efficacy of Zilucoplan in Subjects With Generalized Myasthenia Gravis | Biotech Hunter | Biotech Hunter