Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients

Active, not recruitingOBSERVATIONAL
Enrollment

5

Participants

Timeline

Start Date

November 1, 2019

Primary Completion Date

December 31, 2024

Study Completion Date

December 31, 2024

Conditions
Neuronal Ceroid-LipofuscinosesNeuronal Ceroid Lipofuscinosis CLN2Spinocerebellar Ataxia, Autosomal Recessive 7
Trial Locations (1)

92868

Children's Hospital of Orange County, Orange

All Listed Sponsors
lead

Children's Hospital of Orange County

OTHER

NCT04098211 - Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients | Biotech Hunter | Biotech Hunter