Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients

RecruitingOBSERVATIONAL
Enrollment

40

Participants

Timeline

Start Date

June 12, 2020

Primary Completion Date

June 30, 2026

Study Completion Date

December 31, 2026

Conditions
GM1 Gangliosidosis
Trial Locations (6)

19104

RECRUITING

Children's Hospital of Philadelphia, Philadelphia

94610

RECRUITING

UCSF Benioff Children's Hospital Oakland, Oakland

Unknown

RECRUITING

Hospital de Clínicas de Porto Alegre, Porto Alegre

RECRUITING

Montreal Children's Hospital Research Institute - McGill University, Montreal

RECRUITING

Gazi University, Ankara

ACTIVE_NOT_RECRUITING

UCL Great Ormond Street Institute of Child Health, London

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Passage Bio, Inc.

INDUSTRY

lead

University of Pennsylvania

OTHER