Open-label Study of Anakinra in MPS III

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

24

Participants

Timeline

Start Date

January 30, 2020

Primary Completion Date

July 17, 2022

Study Completion Date

March 8, 2023

Conditions
Mucopolysaccharidosis III
Interventions
BIOLOGICAL

anakinra

anakinra single-use prefilled glass syringes

Trial Locations (1)

90502

The Lundquist Institute at Harbor-UCLA Medical Center, Torrance

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Cure Sanfilippo Foundation

UNKNOWN

collaborator

Swedish Orphan Biovitrum

INDUSTRY

lead

Lynda E Polgreen

OTHER