NCT03910621View on ClinicalTrials.gov

Safety and Efficacy of Miglustat in Chinese NPC Patients

PHASE4CompletedINTERVENTIONAL
Enrollment

17

Participants

Timeline

Start Date

April 2, 2020

Primary Completion Date

March 25, 2022

Study Completion Date

March 25, 2022

Conditions
Niemann-Pick Disease, Type C
Interventions
DRUG

Miglustat

capsule, oral use

Trial Locations (2)

100034

Peking University first Hospital, Beijing

200092

Xin Hua Hospital, Shanghai Jiao Tong University, Shanghai

Sponsors

Lead Sponsor

Actelion
All Listed Sponsors
lead

Actelion

INDUSTRY