60
Participants
Start Date
June 18, 2019
Primary Completion Date
February 10, 2021
Study Completion Date
February 10, 2021
Cysteamine Bitartrate
Cysteamine bitartrate administered four times per day (QID) for 8 weeks. 125mg tablet QID.
Placebo Oral Tablet
Placebo administered for 8 weeks. 125mg tablet QID.
Cincinnati Children's Hospital Medical Center, Cincinnati
Children's Hospital Medical Center, Cincinnati
OTHER