100
Participants
Start Date
December 19, 2019
Primary Completion Date
June 30, 2023
Study Completion Date
June 30, 2023
RECRUITING
Hopital la Timone Enfants, Marseille
RECRUITING
Brest University Hospital Centre, Brest
RECRUITING
University Hospital of Bordeaux, Bordeaux
RECRUITING
CHU Lille, Lille
RECRUITING
Hôpital Hautepierre, Strasbourg
RECRUITING
Hopital Femme Mere Enfant, Bron
RECRUITING
Hôpital Armand Trousseau, Paris
RECRUITING
Great Ormond Street Hospital & University College London Hospital, London
RECRUITING
Institute of Genetic Medicine, Newcastle
Lead Sponsor
Genethon
OTHER