Safety and Efficacy Study of MOD-4023 to Treat Children With Growth Hormone Deficiency

PHASE3CompletedINTERVENTIONAL
Enrollment

44

Participants

Timeline

Start Date

December 7, 2017

Primary Completion Date

March 6, 2020

Study Completion Date

March 6, 2020

Conditions
Growth Hormone Deficiency
Interventions
DRUG

MOD-4023

"MOD-4023 is a long-acting modified recombinant human growth hormone (r-hGH) which utilizes C-terminal peptide (CTP) technology. It will be provided as a solution for injection containing 20 or 50 mg/mL MOD-4023 in a multi-dose disposable pre-filled PEN.~MOD-4023 will be administered as a SC injection once weekly, using a delivery device."

DRUG

Genotropin

"Genotropin® is dispensed in a 2-chamber cartridge. The front compartment contains recombinant somatropin, glycine, mannitol, sodium dihydrogen phosphate anhydrous and disodium phosphate anhydrous. The rear compartment contains m-Cresol and mannitol in water for injections.~A delivery device (Genotropin®) will be used for daily (evening/bedtime) SC administration of Genotropin® into the region of the upper arms, buttocks, thighs or abdomen (8 locations). Injection sites should be rotated.~Dose regimen for Genotropin®: 0.025 mg/kg/day (or 0.175 mg/kg/w divided equally to 7 injections over a week)."

Trial Locations (46)

480-1195

Aichi Medical University Hospital, Nagakute

285-8765

Seirei Sakura Citizen Hospital, Sakura

807-8556

Hospital of the University of Occupational and Environmental Health, Kitakyushu

371-8511

Gunma University Hospital, Maebashi

721-8511

Fukuyama City Hospital, Fukuyama

737-0023

National Hospital Organization Kure Medical Center & Chugoku Cancer Center, Kure

722-8508

Onomichi General Hospital, Onomichi

078-8211

Hokkaido P.W.F.A.C. Asahikawa-Kosei General Hospital, Asahikawa

078-8510

Asahikawa Medical University Hospital, Asahikawa

062-0931

KKR Sapporo Medical Center, Sapporo

650-0017

Kobe University Hospital, Kobe

657-0846

Takahashi Clinic, Kobe

665-0827

Takarazuka City Hospital, Takarazuka

216-8511

St. Marianna University School of Medicine Hospital, Kawasaki

610-0013

National Hospital Organization Minami Kyoto Hospital, Jōyō

980-8508

East Japan Railway Company Sendai Branch Office JR Sendai Hospital, Sendai

980-8574

National University Corporation Tohoku University Tohoku University Hospital, Sendai

981-3203

Igarashi childrens clinic, Sendai

879-5593

Oita University Hospital, Yufu

594-1101

Osaka Women's and Children's Hospital, Izumi

565-0871

Osaka University Hospital, Suita

350-0495

Saitama Medical University Hospital, Iruma-Gun

350-8550

Saitama Medical Center, Kawagoe

693-8501

Shimane University Hospital, Izumo

183-8561

Tokyo Metropolitan Childrens Medical Center, Fuchū

157-8535

National Center for Child Health and Development, Setagaya-Ku

160-8582

Keio University Hospital, Shinjuku

173-8606

Teikyo University Hospital, tabashi City

683-8504

Tottori University Hospital, Yonago

010-8543

Akita University Hospital, Akita

813-0017

Fukuoka Children's Hospital, Fukuoka

501-1194

Gifu University Hospital, Gifu

730-8518

Hiroshima City Hospital Organization Hiroshima City Hiroshima Citizens Hospital, Hiroshima

860-8556

Kumamoto University Hospital, Kumamoto

880-8510

Miyazaki Prefectural Miyazaki Hospital, Miyazaki

381-0025

Arakawa Children's Clinic, Nagano

630-8054

Nara Prefecture General Medical Center, Nara

951-8520

Niigata University Medical & Dental Hospital, Niigata

700-0013

Okayama Saiseikai General Hospital Outpatient Center, Okayama

701-1192

National Hospital Organization Okayama Medical Center, Okayama

534-0021

Osaka City General Hospital, Osaka

545-8586

Osaka City University Hospital, Osaka

330-8777

Saitama Childrens Medical Center, Saitama

336-8522

Saitama City Hospital, Saitama

420-8660

Shizuoka Childrens Hospital, Shizuoka

105-8470

Toranomon Hospital, Tokyo

All Listed Sponsors
lead

OPKO Health, Inc.

INDUSTRY

NCT03874013 - Safety and Efficacy Study of MOD-4023 to Treat Children With Growth Hormone Deficiency | Biotech Hunter | Biotech Hunter