Nutrition Status of Adults With PKU Before and During Treatment With Pegvaliase

CompletedOBSERVATIONAL
Enrollment

12

Participants

Timeline

Start Date

March 8, 2019

Primary Completion Date

December 31, 2022

Study Completion Date

October 20, 2023

Conditions
Phenylketonurias
Trial Locations (1)

02115

Boston Children's Hospital, Boston

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

BioMarin Pharmaceutical

INDUSTRY

lead

Boston Children's Hospital

OTHER