Nutritional Status in Phenylketonuria

CompletedOBSERVATIONAL
Enrollment

94

Participants

Timeline

Start Date

January 7, 2019

Primary Completion Date

September 10, 2019

Study Completion Date

September 10, 2019

Conditions
Phenylketonurias
Interventions
OTHER

Diet

A specific dietary treatment for patients with Phenylketonuria.

DRUG

Sapropterin

A pharmacological treatment for patients with Phenylketonuria, used alone or in combination with dietary treatment.

Trial Locations (1)

4099-001

Centro Hospitalar Universitário do Porto, Porto

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Centro Hospitalar do Porto

OTHER

collaborator

BioMarin Pharmaceutical

INDUSTRY

lead

Universidade do Porto

OTHER