Evaluation of a Treatment With Allopurinol in Adenylosuccinate Lyase Deficiency

PHASE2CompletedINTERVENTIONAL
Enrollment

8

Participants

Timeline

Start Date

October 14, 2019

Primary Completion Date

June 17, 2022

Study Completion Date

June 17, 2022

Conditions
Adenylosuccinate Lyase Deficiency
Interventions
DRUG

Allopurinol

Daily oral administration

Trial Locations (2)

75013

LA PITIE-SALPETRIERE Hospital, AP-HP, Paris

75015

Department of Pediatry. Reference centre of Hereditary diseases of the metabolism of child and adult. Necker - Enfants malades Hospital, Paris

All Listed Sponsors
collaborator

URC-CIC Paris Descartes Necker Cochin

OTHER

lead

Assistance Publique - Hôpitaux de Paris

OTHER

NCT03776656 - Evaluation of a Treatment With Allopurinol in Adenylosuccinate Lyase Deficiency | Biotech Hunter | Biotech Hunter