15
Participants
Start Date
September 4, 2018
Primary Completion Date
September 30, 2019
Study Completion Date
March 18, 2021
VPRIV
VPRIV (Velaglucerase alfa) Long-term enzyme replacement therapy (ERT) for patients with type 1 Gaucher disease.
Michal Becker- Cohen, Jerusalem
Shaare Zedek Medical Center
OTHER