NCT03694561View on ClinicalTrials.gov

"Developing a Management Approach for Patients With Late-Onset Pompe Disease"

Active, not recruitingOBSERVATIONAL

Enrollment

20

Participants

Timeline

Start Date

March 25, 2019

Primary Completion Date

August 31, 2027

Study Completion Date

August 31, 2027

Conditions

Pompe DiseasePompe Disease (Late-onset)GAA Deficiency

Interventions

OTHER

Observational

This study is a systematic investigation of the natural history of late-onset Pompe disease in infancy and childhood

Trial Locations (1)

27705

Duke University, Durham

Sponsors

Lead Sponsor

Duke University

All Listed Sponsors

collaborator

Genzyme, a Sanofi Company

INDUSTRY

lead

Duke University

OTHER