782
Participants
Start Date
July 16, 2018
Primary Completion Date
December 31, 2032
Study Completion Date
December 31, 2032
No intervention
Access to any treatment is through authorized commercial use and not as a part of this DMP
Children's Hospital of Philadelphia, Philadelphia
Johns Hopkins University, Baltimore
University of Virgina School of Medicine, Charlottesville
Children's Hospital of The King's Daughter, Norfolk
Duke University, Durham
Children's Hospital of Alabama, Birmingham
Vanderbilt University - Department of Medicine, Nashville
Vanderbilt University - Department of Pediatrics, Nashville
Nationwide Children's Hospital, Columbus
The Ohio State University Wexner Medical Center, Columbus
Cincinnati Children's Hospital, Cincinnati
American Family Children's Hospital, Madison
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University School of Medicine, St Louis
Houston Methodist Research Institute, Houston
University of Texas, Health Science Center, Houston
Children's Hospital of Colorado, Aurora
Children's Hospital Los Angeles, Los Angeles
Rady Children's Hospital San Diego, San Diego
University of California San Francisco, San Francisco
Seattle Children's Hospital, Seattle
Yale University School of Medicine, New Haven
Indiana University School of Medicine, Indianapolis
Boston Children's Hospital, Boston
Hospital General de Niños Pedro de Elizalde, Buenos Aires
Hospital de Niños Dr. Ricardo Gutierrez, Buenos Aires
Hospital Privado Universitario de Córdoba, Córdoba
Pontificia Universidad Católica de Chile, Santiago
Hospital Universitario de San Vicente Fundación, Medellín
Hospital Infantil Universitario de San José, Bogotá
Hospital Universitário Alcides Carneiro (HUAC), São José
Instituto de Medicina Avancada (IMA Brasil), São Paulo
CETI - Centro de Estudos em Terapias Inovadoras, Curitiba
Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo, São Paulo
British Columbia Children's Hospital, Vancouver
Bone Research and Education Centre, Oakville
Shiner's Hospital for Children - Canada, Montreal
Children's Hospital Eastern Ontario Research Institute, Ottawa
Kyowa Kirin Co., Ltd.
INDUSTRY
Ultragenyx Pharmaceutical Inc
INDUSTRY