X-linked Hypophosphatemia Disease Monitoring Program

Active, not recruitingOBSERVATIONAL
Enrollment

782

Participants

Timeline

Start Date

July 16, 2018

Primary Completion Date

December 31, 2032

Study Completion Date

December 31, 2032

Conditions
X-linked HypophosphatemiaHypophosphatemic Rickets
Interventions
OTHER

No intervention

Access to any treatment is through authorized commercial use and not as a part of this DMP

Trial Locations (38)

19104

Children's Hospital of Philadelphia, Philadelphia

21218

Johns Hopkins University, Baltimore

22903

University of Virgina School of Medicine, Charlottesville

23507

Children's Hospital of The King's Daughter, Norfolk

27708

Duke University, Durham

35233

Children's Hospital of Alabama, Birmingham

37212

Vanderbilt University - Department of Medicine, Nashville

37232

Vanderbilt University - Department of Pediatrics, Nashville

43205

Nationwide Children's Hospital, Columbus

The Ohio State University Wexner Medical Center, Columbus

45229

Cincinnati Children's Hospital, Cincinnati

53792

American Family Children's Hospital, Madison

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

63110

Washington University School of Medicine, St Louis

77030

Houston Methodist Research Institute, Houston

University of Texas, Health Science Center, Houston

80045

Children's Hospital of Colorado, Aurora

90027

Children's Hospital Los Angeles, Los Angeles

92123

Rady Children's Hospital San Diego, San Diego

94158

University of California San Francisco, San Francisco

98105

Seattle Children's Hospital, Seattle

06520

Yale University School of Medicine, New Haven

46202-5167

Indiana University School of Medicine, Indianapolis

02115

Boston Children's Hospital, Boston

C1270AAN

Hospital General de Niños Pedro de Elizalde, Buenos Aires

C1425EFD

Hospital de Niños Dr. Ricardo Gutierrez, Buenos Aires

Unknown

Hospital Privado Universitario de Córdoba, Córdoba

Pontificia Universidad Católica de Chile, Santiago

Hospital Universitario de San Vicente Fundación, Medellín

Hospital Infantil Universitario de San José, Bogotá

58400-398

Hospital Universitário Alcides Carneiro (HUAC), São José

05437-000

Instituto de Medicina Avancada (IMA Brasil), São Paulo

80030-110

CETI - Centro de Estudos em Terapias Inovadoras, Curitiba

05403-000

Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo, São Paulo

V6H 3N1

British Columbia Children's Hospital, Vancouver

ON L6M 1M1

Bone Research and Education Centre, Oakville

H4A 0A9

Shiner's Hospital for Children - Canada, Montreal

K1H 5B2

Children's Hospital Eastern Ontario Research Institute, Ottawa

All Listed Sponsors
collaborator

Kyowa Kirin Co., Ltd.

INDUSTRY

lead

Ultragenyx Pharmaceutical Inc

INDUSTRY

NCT03651505 - X-linked Hypophosphatemia Disease Monitoring Program | Biotech Hunter | Biotech Hunter