Study Assessing PTI-428 Safety, Tolerability, Pharmacokinetics and Effect in Subjects With Cystic Fibrosis

PHASE2CompletedINTERVENTIONAL
Enrollment

40

Participants

Timeline

Start Date

August 21, 2018

Primary Completion Date

February 18, 2019

Study Completion Date

February 18, 2019

Conditions
Cystic Fibrosis
Interventions
DRUG

PTI-428

Active

DRUG

Placebo

Placebo

Trial Locations (26)

10003

Mount Sinai Beth Israel, New York

10032

Columbia University Medical Center, New York

10595

New York Medical College, Valhalla

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

27710

Duke University Medical Center, Durham

29425

Medical University of South Carolina, Charleston

32701

Central Florida Pulmonary Group, Altamonte Springs

35233

University of Alabama at Birmingham, Birmingham

40202

Universitey of Louisville, Kosair Charities Pediatric Clinical Research Unit, Louisville

43205

Nationwide Children's Hospital, Columbus

44308

Akron Children's Hospital, Akron

48109

Michigan Medicine, University of Michigan, Ann Arbor

52242

University of Iowa, Roy J and Lucille A Carver College of Medicine, Iowa City

55455

University of Minnesota, Minneapolis

60611

Northwestern University, Chicago

61637

Cystic Fibrosis Center, Children's Hospital of Illinois at OSF Saint Francis Medical Center, Peoria

64108

Children's Mercy Hospital, Kansas City

75708

The University of Texas Health Science Center at Tyler - Center for Clinical Research, Tyler

80206

National Jewish Health, Denver

84132

University of Utah, Salt Lake City

85724

University of Arizona, Tucson

94305

Stanford University, Stanford

04102

Maine Medical Center, Portland

02114

Massachusetts General Hospital, Boston

02115

Boston Children's Hospital, Boston

03104

Dartmouth Hitchcock Medical Center, Manchester

All Listed Sponsors
lead

Proteostasis Therapeutics, Inc.

INDUSTRY

NCT03591094 - Study Assessing PTI-428 Safety, Tolerability, Pharmacokinetics and Effect in Subjects With Cystic Fibrosis | Biotech Hunter | Biotech Hunter