30
Participants
Start Date
November 1, 2018
Primary Completion Date
August 31, 2019
Study Completion Date
August 31, 2019
University of Minnesota, Minneapolis
Rare Diseases Clinical Research Network
NETWORK
National Center for Advancing Translational Sciences (NCATS)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NIH
Lysosomal Disease Network
OTHER
University of Minnesota
OTHER