Open Label Extension Study of 1 mg/kg Pegunigalsidase Alfa Every 2 Weeks in Patients With Fabry Disease

PHASE3CompletedINTERVENTIONAL
Enrollment

97

Participants

Timeline

Start Date

September 16, 2018

Primary Completion Date

January 21, 2025

Study Completion Date

January 21, 2025

Conditions
Fabry Disease
Interventions
DRUG

pegunigalsidase alfa

Recombinant human alpha galactosidase A

Trial Locations (30)

1083

Semmelweis Egyetem, Budapest

2380

General Hospital Slovenj Gradec, Slovenj Gradec

3050

Royal Melbourne Hospital, Parkville

5021

Haukeland University Hospital Klinisk Forskningspost, Bergen

12808

Vseobecna fakultni nemocnice v Praze, Prague

15224

University of Pittsburgh, Pittsburgh

22030

O+O Alpan LLC, Fairfax

30322

Emory University School of Medicine, Atlanta

32610

University of Florida, Gainesville

35233

UAB Medicine, Birmingham

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

49525

Infusion Associates, Grand Rapids

50012

Hospital de Dia Quiron Zaragoza, Zaragoza

52242

University of Iowa Hospitals and Clinics, Iowa City

53226

Medical College of Wisconsin, Milwaukee

75235

Renal Disease Research Institute, LLC - Dallas, Dallas

75246

Institute of Metabolic Disease, Dallas

80131

"Azienda Ospedaliera Universitaria Federico II", Napoli

84108

University of Utah Hospitals & Clinics, Salt Lake City

85016

Phoenix Children's Hospital, Phoenix

92037

University of California San Diego, La Jolla

92380

Hospital Raymond-Poincaré, Garches

92868

University of California Irvine Center, Orange

B3H 1V8

Capital District Health Authority, Halifax

FI-20521

Turku University Central Hospital, Turku

1105 AZ

Academisch Medisch Centrum, Amsterdam

B152TH

University Hospitals Birmingham NHS Foundation Trust, Queen Elizabeth Hospital, Edgbaston

M6 8HD

Salford Royal, Salford

CB2 0QQ

Addenbrooke's Hospital, Cambridge

NW3 2QG

The Royal Free Hospital, London

All Listed Sponsors
lead

Chiesi Farmaceutici S.p.A.

INDUSTRY

NCT03566017 - Open Label Extension Study of 1 mg/kg Pegunigalsidase Alfa Every 2 Weeks in Patients With Fabry Disease | Biotech Hunter | Biotech Hunter