Natural History of Pompe Disease

RecruitingOBSERVATIONAL
Enrollment

20

Participants

Timeline

Start Date

June 7, 2019

Primary Completion Date

March 31, 2033

Study Completion Date

March 31, 2033

Conditions
Glycogen Storage Disease Type II, Adult
Trial Locations (1)

92380

RECRUITING

Hôpital Raymond Poincaré, Garches

All Listed Sponsors
lead

Assistance Publique - Hôpitaux de Paris

OTHER