A Study of Fitusiran in Severe Hemophilia A and B Patients Previously Receiving Factor or Bypassing Agent Prophylaxis

PHASE3CompletedINTERVENTIONAL
Enrollment

80

Participants

Timeline

Start Date

July 25, 2018

Primary Completion Date

January 20, 2022

Study Completion Date

March 25, 2022

Conditions
Hemophilia
Interventions
DRUG

Fitusiran

Pharmaceutical form: solution for injection Route of administration: subcutaneous

DRUG

BPA prophylaxis

Pharmaceutical form: solution for injection Route of administration: Intravenous

DRUG

Factor (FVIII or FIX) prophylaxis

Pharmaceutical form: solution for injection Route of administration: Intravenous

Trial Locations (35)

12

Investigational Site Number 5301, Crumlin

2100

Investigational Site Number 4501, Copenhagen

3181

Investigational Site Number 6104, Prahran

3722

Investigational Site Number 8204, Seoul

20122

Investigational Site Number 3902, Milan

27100

Investigational Site Number 9008, Gaziantep

34093

Investigational Site Number 9005, Istanbul

35040

Investigational Site Number 9010, Izmir

35233

Investigational Site Number 8202, Daejeon

38039

Investigational Site Number 9009, Kayseri

52621

Investigational Site Number 9701, Ramat Gan

55200

Investigational Site Number 9006, Samsun

65080

Investigational site number 9013, Van

68000

Investigational Site Number 6004, Ampang

69677

Investigational Site Number 3303, Lyon

79044

Investigational Site Number 8002, Lviv

80100

Investigational Site Number 6002, Johor Bahru

88586

Investigational Site Number 6003, Kota Kinabalu

90027

Investigational Site Number 0139, Los Angeles

100045

Investigational Site Number 8604, Beijing

Unknown

Investigational Site Number 8101, Nagoya

Investigational Site Number 8102, Nishinomiya

Investigational Site Number 8104, Saitama

Investigational Site Number 8109, Tokyo

Investigational Site Number 5201, San Pablo

602-739

Investigational Site Number 8201, Busan

?01130

Investigational Site Number 9002, Adana

06100

Investigational Site Number 9001, Ankara

07059

Investigational Site Number 9004, Antalya

TR-35100

Investigational Site Number 9003, Izmir

?01135

Investigational Site Number 8003, Kyiv

G4 0SF

Investigational Site Number 4402, Glasgow

E1 2ES

Investigational Site Number 4407, London

NW3 2QG

Investigational Site Number 4403, London

SE1 9RT

Investigational Site Number 4401, London

All Listed Sponsors
lead

Genzyme, a Sanofi Company

INDUSTRY

NCT03549871 - A Study of Fitusiran in Severe Hemophilia A and B Patients Previously Receiving Factor or Bypassing Agent Prophylaxis | Biotech Hunter | Biotech Hunter