Mucopolysaccharidosis Type II Natural History

CompletedOBSERVATIONAL
Enrollment

36

Participants

Timeline

Start Date

September 27, 2017

Primary Completion Date

March 22, 2022

Study Completion Date

March 22, 2022

Conditions
Mucopolysaccharidosis II
Trial Locations (3)

15224

Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders, Pittsburgh

90035-903

Hospital de Clinicas de Porto Alegre, Porto Alegre

Unknown

Manchester Centre for Genomic Medicine, Manchester

All Listed Sponsors
lead

REGENXBIO Inc.

INDUSTRY

NCT03529786 - Mucopolysaccharidosis Type II Natural History | Biotech Hunter | Biotech Hunter