36
Participants
Start Date
September 27, 2017
Primary Completion Date
March 22, 2022
Study Completion Date
March 22, 2022
Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders, Pittsburgh
Hospital de Clinicas de Porto Alegre, Porto Alegre
Manchester Centre for Genomic Medicine, Manchester
REGENXBIO Inc.
INDUSTRY