Gentamicin for Junctional Epidermolysis Bullosa

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

6

Participants

Timeline

Start Date

June 1, 2018

Primary Completion Date

July 30, 2020

Study Completion Date

August 31, 2020

Conditions
Junctional Epidermolysis Bullosa
Interventions
DRUG

Gentamicin Sulfate

Gentamicin (formulated as gentamicin sulfate) is a well-known, well-characterized antibiotic that has been used for four decades as a treatment against gram negative bacteria. It, like other aminoglycoside antibiotics, has the well documented added potential to facilitate readthrough of premature termination codons in eukaryotic cells and organisms.

Trial Locations (1)

90033

RECRUITING

University of Southern California, Los Angeles

All Listed Sponsors
lead

University of Southern California

OTHER