36
Participants
Start Date
January 24, 2018
Primary Completion Date
March 6, 2019
Study Completion Date
March 6, 2019
WVE-210201
WVE-210201 is a stereopure antisense oligonucleotide (ASO)
Placebo
Sodium Chloride
UZ Gent, Ghent
U.O. Immunologia Pediatrica, Milan
Rare Disease Research, LLC., Atlanta
U.O.C di Neurologia e Malattie Neuromuscolari Centro Clinico Nemo Sud, Messina
Universitaire Ziekenhuizen Leuven, Leuven
CHR de la Citadelle, Liège
London Health Sciences Centre - Hospital, London
Hôpital Armand Trousseau, Paris
University Hospitals Bristol NHS Foundation Trust, Bristol
UCL Institute of Child Health & Great Ormond Street Hospital for Children, London
Radbound University Nijmegen Medical Care, Nijmegen
Alder Hey Children's Hospital, Liverpool
Evelina London Children's Hospital, London
Wave Life Sciences Ltd.
INDUSTRY