A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients With Inhibitors

PHASE3CompletedINTERVENTIONAL
Enrollment

60

Participants

Timeline

Start Date

February 14, 2018

Primary Completion Date

November 25, 2020

Study Completion Date

June 23, 2021

Conditions
Hemophilia AHemophilia B
Interventions
DRUG

fitusiran

solution for injection; by subcutaneous (SC) injection

DRUG

Bypassing agents

solution for injection; by intravenous (IV) injection

Trial Locations (58)

110

Investigational Site Number 8801, Taipei

500

Investigational Site Number 8803, Changhua

699

Investigational Site Number 2703, Polokwane

2050

Investigational Site Number 6101, Camperdown

2193

Investigational Site Number 2701, Parktown

3168

Investigational Site Number 6104, Clayton

3722

Investigational Site Number 8203, Seoul

4103

Investigational Site Number 4906, Leipzig

6001

Investigational Site Number 2702, Port Elizabeth

21205

Investigational Site Number 0136, Baltimore

28046

Investigational Site Number 3402, Madrid

32207

Investigational Site Number 0115, Jacksonville

32610

Investigational Site Number 0128, Gainesville

33136

Investigational Site Number 0105, Miami

33607

Investigational Site Number 0103, Tampa

34093

Investigational Site Number 9005, Istanbul

35100

Investigational Site Number 9003, Izmir

35128

Investigational Site Number 3904, Padua

35233

Investigational Site Number 8202, Daejeon

50134

Investigational Site Number 3901, Florence

60590

Investigational Site Number 4905, Frankfurt am Main

69677

Investigational Site Number 3303, Lyon

70112

Investigational Site Number 0119, New Orleans

76038

Investigational Site Number 3301, Rouen

79044

Investigational Site Number 8002, Lviv

85016

Investigational Site Number 0117, Phoenix

88586

Investigational Site Number 6003, Kota Kinabalu

89135

Investigational Site Number 0111, Las Vegas

90027

Investigational Site Number 0139, Los Angeles

92123

Investigational Site Number 0137, San Diego

92868

Investigational Site Number 0135, Orange

100045

Investigational Site Number 8604, Beijing

200025

Investigational Site Number 8603, Shanghai

226003

Investigational Site Number 9106, Lucknow

300020

Investigational Site Number 8601, Tianjin

302017

Investigational Site Number 9104, Jaipur

310003

Investigational Site Number 8605, Hangzhou

411001

Investigational Site Number 9103, Pune

411004

Investigational Site Number 9111, Pune

510515

Investigational Site Number 8602, Guangzhou

560034

Investigational Site Number 9102, Bangalore

632004

Investigational Site Number 9105, Vellore

19104-5127

Investigational Site Number 0104, Philadelphia

H1T 2M4

Investigational Site Number 1102, Montreal

Unknown

Investigational Site Number 9108, India

Investigational Site Number 8110, Japan

Investigational Site Number 8103, Kita Kyushu-Shi

Investigational Site Number 6004, Malaysia

Investigational Site Number 8204, Seoul

Investigational Site Number 8804, Dawan

Investigational Site Number 8805, Dawan

Investigational Site Number 9006, Turkey

?01130

Investigational Site Number 9002, Adana

07059

Investigational Site Number 9004, Akdeniz

06100

Investigational Site Number 9001, Ankara

01135

Investigational Site Number 8003, Kyiv

04060

Investigational Site Number 8001, Kyiv

E1 2ES

Investigational Site Number 4407, London

All Listed Sponsors
lead

Genzyme, a Sanofi Company

INDUSTRY

NCT03417102 - A Study of Fitusiran (ALN-AT3SC) in Severe Hemophilia A and B Patients With Inhibitors | Biotech Hunter | Biotech Hunter