Natural History Study of CEP290-Related Retinal Degeneration

CompletedOBSERVATIONAL
Enrollment

26

Participants

Timeline

Start Date

December 17, 2017

Primary Completion Date

May 6, 2022

Study Completion Date

May 6, 2022

Conditions
BlindnessLeber Congenital Amaurosis 10Vision DisordersEye DiseasesEye Diseases, HereditaryEye Disorders CongenitalRetinal DiseaseRetinal Degeneration
Trial Locations (7)

6525

Radboud Universitair Medisch Centrum, Nijmegen

33136

Bascom Palmer Eye Institute, Miami

35392

Universitaetsklinikum Giessen and Marburg GmbH, Giessen

48105

W.K. Kellogg Eye Center, Ann Arbor

75252

Universite Pierre et Marie Curie, Paris

97239

Casey Eye Institute - OHSU, Portland

02114

Massachusetts Eye and Ear Infirmary, Boston

Sponsors
All Listed Sponsors
lead

Editas Medicine, Inc.

INDUSTRY

NCT03396042 - Natural History Study of CEP290-Related Retinal Degeneration | Biotech Hunter | Biotech Hunter