52
Participants
Start Date
October 13, 2017
Primary Completion Date
December 28, 2023
Study Completion Date
May 30, 2024
TAK-755
Participants in prophylaxis cohort will receive IV infusions of 40 IU/kg TAK-755 ORT during Period 1 and Period 2 and switch to TAK-755 SIN during Period 3 for six months once in a week or twice in a week. In On-demand cohort participants will receive daily IV dose of TAK-755.
Standard of care
Participants will receive Investigator-recommended Standard of care (SoC).
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma
AKH - Medizinische Universität Wien, Vienna
Hospital General Universitario de Alicante, Alicante
Complejo Hospitalario Universitario A Coruña, A Coruña
Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico, Milan
Universitaetsklinikum Hamburg-Eppendorf, Hamburg
Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII (Presidio Papa Giovanni XXIII), Bergamo
Duke University Medical Center, Durham
Winship Cancer Institute, Atlanta
Hospital Universitario de Salamanca, Salamanca
Hospital Universitario Virgen del Rocio, Seville
CHU Saint Etienne - Hôpital Nord, Saint-Priest-en-Jarez Cedex
Ohio State Univ College Of Medicine, Columbus
Cincinnati Children's Hospital Medical Center, Cincinnati
Hospital Universitari i Politecnic La Fe, Valencia
Hospital de Cruces, Barakaldo
Hopital Claude Huriez - CHU Lille, Lille
University of Oklahoma, Oklahoma City
Hôpital Necker - Enfants Malades, Paris
Hôpital Robert Debré - Paris, Paris
Hôpital Saint-Antoine, Paris
The Methodist Hospital, Houston
Alliance for Childhood Diseases, Cure 4 the Kids Foundation, Las Vegas
"Azienda Ospedaliera Universitaria Policlinico - Vittorio Emanuele (Presidio Ferrarotto Alessi)", Catania
Universitaetsklinikum Jena, Jena
"Dipartimento di Medicina Traslazionale e di Precisione - Sapienza Universita di Roma", Rome
Kyushu University Hospital, Fukuoka
Hyogo College of Medicine Hospital, Nishinomiya-shi
Medical Hospital, Tokyo Medical and Dental University, Bunkyō City
Samodzielny Publiczny Dzieciecy Szpital Kliniczny, Warsaw
Instytut Hematologii i Transfuzjologii, Warsaw
University College London Hospitals, London
Royal Manchester Children's Hospital, Manchester
Takeda Development Center Americas, Inc.
INDUSTRY
Baxalta now part of Shire
INDUSTRY