European Registry of Patients With Infantile-onset Spinal Muscular Atrophy

CompletedOBSERVATIONAL
Enrollment

100

Participants

Timeline

Start Date

October 10, 2017

Primary Completion Date

November 15, 2020

Study Completion Date

November 15, 2020

Conditions
Spinal Muscular Atrophy
Trial Locations (6)

Unknown

Hopital Morvan - CHU de Brest, Brest

"Service de Rééducation Pédiatrique Infantile L'Escale - Hôpital Femme Mère Enfant", Bron

Hôpital le Bocage - CHU Dijon, Dijon

Maladie Neuromusculaire de l'enfant - Service Maladies infectieuses et neurologie infantile - Hôpital Roger Salengro, Lille

I-Motion Institute, Paris

Unité de neurologie pédiatrique - Hôpital des enfants, Toulouse

All Listed Sponsors
lead

Institut de Myologie, France

OTHER

NCT03339830 - European Registry of Patients With Infantile-onset Spinal Muscular Atrophy | Biotech Hunter | Biotech Hunter