195
Participants
Start Date
September 5, 2017
Primary Completion Date
November 19, 2020
Study Completion Date
November 19, 2020
Emicizumab
Initial dosing will be 3 mg/kg/week subcutaneously for 4 weeks; Maintenance dosing will follow at 1.5 mg/kg/week subcutaneously for the remainder of the 2-year treatment period
Magyar Honvédség Egészségügyi Központ; Országos Haemophilia Központ, Budapest
Royal Prince Alfred Hospital; Haematology, Camperdown
UZ Leuven Gasthuisberg, Leuven
Alfred Hospital, Melbourne
Inselspital Bern; Hämatologie und Hämatologisches Zentrallabor, Bern
Fiona Stanley Hospital, Murdoch
University of Pecs, I st Dept of Internal Medicine, Pécs
Országos Vérellátó Szolgálat - Győri Regionális Vérellátó Központ, Győr
AO Città Salute e Scienza D-Osp S. G. Battista Molinette; SSCVD Malattie Tromboti e Emorragiche, Turin
Vivantes Klinikum im Friedrichshain - Landsberger Allee, Angiologie und Hämostaseologie, Berlin
King Faisal Specialist Hospital & Research Centre; Oncology, Riyadh
"IRCCS Ca' Granda Ospedale Maggiore Policlinico; Centro Emofilia e Trombosi Angelo Bianchi e Bonomi", Milan
Hospital Universitario la Paz; Servicio de Hematologia, Madrid
Hospital Regional Universitario Carlos Haya; Servicio de Hematologia, Málaga
Azienda Ospedaliera di Padova; Centro Emofilia, Padua
AOU Policlinico S. Orsola Malpighi; U.O. Angiologia e Malattie della Coagulazione Marino Golinelli, Bologna
Hospital Universitario Virgen del Rocio; Servicio de Hematologia, Seville
AOU di Parma; Dip Emergenza-Urgenza Centro Riferimento Regionale per l'emofilia, Parma
Hospital Universitario la Fe; Servicio de Hematologia, Valencia
AOU Careggi; SOD Malattie Emorragiche, Florence
Universitätsklinikum Bonn; Institut für Experimentelle Hämatologie und Transfusionsmedizin, Bonn
Hämophiliezentrum Med. Klinik III/Institut für Transfusionsmedizin; Johann Wolfgang Goethe-Univers., Frankfurt/M.
Hämophilie-Zentrum Rhein Main GmbH, Mörfelden-Walldorf
AOU Federico II; Medicina Clinica Chirurgia Centro Emocoaugulopatie e Emofilia, Napoli
Klinikum der Universität München, Campus Innenstadt; Hämostaseologische Ambulanz/Hämophiliezentrum, München
Azienda Uni Ria Policlinico P. Giaccone ; Divisione Di Ematologia E Trapianto, Palermo
Centro de Atención e Investigación Médica CAIMED S.A.S, Localidad Puente Aranda
Morozov Children's Municipal Clinical Hospital. Haematology department, Moscow
"Hematological Scientific Center", Moscow
City Outpatient Clinic #37, City Hemophilia Treatment Center, Saint Petersburg
Louis Turcanu Emergency Clinical Hospital for Children; First Pediatric Clinic, Timișoara
King Edward Memorial Hospital and Seth G.S. Medical College; Department of Hematology, Mumbai
Fortis Hospitals Limited, Mumbai
Grant Medical Foundation, Ruby Hall Clinic, Pune
Sahyadri Speciality Hospital; Hematology & Bone Marrow Unit, Pune
Samara State Medical University, Samara
St. John's Medical College & Hospital; Department of Medicine, Bengaluru
Christian Medical College & Hospital; Department of Haematology, Vellore
"Regional State Budgetary Institution of Healthcare Regional Cinilcal Hospital; Pulmonology", Barnaul
Nil Ratan Sircar Medical College and Hospital; Department of Hematology, Kolkata
Sheba Medical Center - National Hemophilia Center, Tel Litwinsky
Centro de Hematologia E Hemoterapia Do Parana - Hemepar, Curitiba
Instituto Estadual de Hema, Rio de Janeiro
Hospital das Clinicas - UNICAMP, Campinas
Faculdade de Medicina de Ribeirão Preto - Universidade de Sao Paulo, Ribeirão Preto
Kaye Edmonton Clinic, Edmonton
CancerCare Manitoba; Neuro-Oncology, Winnipeg
McMaster University Health Sciences Center, Hamilton
St. Michael's Hospital, Toronto
Hospital Pablo Tobon Uribe, Medellín
Helsingin yliopistollinen keskussairaala, Meilahden sairaala, Helsinki
Universitätsklinikum Leipzig, Innere Medizin, Neurologie, Dermatologie; Zentrum für Hämostaseologie, Leipzig
Oncomedica, Guatemala City
Universita' Degli Studi La Sapienza-Ist.Di Ematologia; Dip Biot Cel e Ematol, Rome
Hospital General de México, Distrito Federal
CENTRO MEDICO NACIONAL SIGLO XXI; Banco de Sangre, Mexico City
Hospital de Especialidades Centro Medico Nacional La Raza; Haematology, Mexico City
Erasmus MC / location Sophia Kinderziekenhuis, Rotterdam
Universitair Medisch Centrum Utrecht, Utrecht
Complejo Hospitalario Arnulfo Arias Madrid; Servicio de Hematología, Panama City
Instytut Hematologii i Transfuzjologii; Klinika Zaburzeń Hemostazy i Chorób Wewnętrznych, Warsaw
Hospital Geral; Servico de Imuno-Hemoterapia, Coimbra
Hospital de Santa Maria; Servico de Imuno-Hemoterapia; Servico de Imuno-Hemoterapia, Lisbon
Hospital de Sao Joao; Servico de Imuno-Hemoterapia; Servico de Imuno-Hemoterapia, Porto
Hospital Universitario Vall de Hebron; Unidad de Hemofília, Barcelona
Sahlgrenska Universitetssjukhuset; Koagulationscentrum, Gothenburg
Karolinska Universitetssjukhuset; Koagulationsmottagningen, Solna
University Hospitals Birmingham NHS Foundation Trust, Birmingham
The Royal London Hospital, London
Royal Free Hospital, London
Royal Victoria Infirmary; Non-Malignant Haematology Research, Newcastle upon Tyne
Royal Hallamshire Hospital Sheffield Teaching Hospitals NHS Foundation Trust, Sheffield
Hoffmann-La Roche
INDUSTRY