360
Participants
Start Date
July 6, 2017
Primary Completion Date
March 5, 2022
Study Completion Date
July 25, 2023
Ataluren
10, 20 mg/kg
PLACEBO
10, 20 mg/kg
UMHAT Sofiamed, Sofia
The Childrens Hospital at Westmead, Westmead
The Royal Childrens Hospital, Parkville
Seoul National University Hospital, Seoul
Perth Children's Hospital, Nedlands
National Taiwan University Hospital, Taipei
Columbia University College of Physicians & Surgeons, New York
Siriraj Hospital, Bangkok
Instituto Nacional de Rehabilitacion, Tlalpan
University of Pittsburgh School of Medicine, Pittsburgh
Children's Hospital of the King's Daughters, Norfolk
Hospital Angeles Chihuahua, Chihuahua City
Northwest Florida Clinical Research Group, LLC, Gulf Breeze
Istanbul University- Instanbul Medical Faculty, Istanbul
Cincinnati Children's Hospital Medical Center, Cincinnati
Indiana University Health - Riley Child Neurology, Indianapolis
University of Michigan - CS Mott Children's Hospital, Ann Arbor
Children's Hospital of Michigan, Detroit
Hospital Tunku Azizah Kuala Lumpur, Kuala Lumpur
Pusan National University Yangsan Hospital, Yangsan
University of Minnesota, Minneapolis
University Malaya Medical Centre (UMMC), Pantai
University of Kansas Medical Center, Kansas City
Cook Childrens Medical Center, Fort Worth
Texas Children's Hospital, Houston
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
University Of Utah, Salt Lake City
Phoenix Childrens Hospital, Phoenix
Children's Hospital of Los Angeles, Los Angeles
Loma Linda University Children's Hospital, San Bernardino
University of California, San Francisco (UCSF) - Benioff Children's Hospital - Oakland, Oakland
Stanford University Medical Center, Palo Alto
University of California (UC) Davis Medical Center, Sacramento
Shriners Hospital for Children, Portland
Seattle Children's Hospital, Seattle
General Hospital of Chinese Armed Police Forces, Beijing
All India Institute of Medical Sciences, New Delhi
Russian National Research Medical University n.a. N.I.Pirogov, structural branch - Research Clinical Institute of Pediatrics n.a. Academician Yu. E. Veltishchev, Moscow
Postgraduate Institute of Medical Education and Research, Chandigarh
"Saint Petersburg State Paediatric Medical University based at Consultative and Diagnostic Centre", Saint Petersburg
Children's Hospital of Fudan University, Shanghai
The First Affiliated Hospital of Fujian Medical University, Fuzhou
Panchshil Hospital, Ahmedabad
P.D. Hinduja Hospital, Māhīm
Xiangya Hospital Central South University, Hunan
Nizam's Institute of Medical Sciences (NIMS), Hyderabad
Shenzhen Children's Hospital, Shenzhen
National Institute of Mental Health and Neurosciences, Bengaluru
Apollo Children's Hospital Chennai, Chennai
Christian Medical College Hospital Vellore, Vellore
Apollo Gleneagles Hospital, Kolkata
University of Texas Health Science Center at San Antonio, San Antonio
Queensland Children's Hospital, South Brisbane
Hospital de Clínicas da Universidade Federal de Minas Gerais, Belo Horizonte
Universidade Federal do Rio de Janeiro, Rio de Janeiro
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo - FMUSP, São Paulo
Childrens Hospital London Health Sciences Centre, London
Childrens Hospital of Eastern Ontario, Ottawa
Queen Mary Hospital, Hong Kong
PTC Clinical Site, Multiple Locations
Instituto Nacional de Pediatría, Mexico City
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie, Warsaw
University of Puerto Rico - School of Medicine, San Juan
Samsung Medical Center, Seoul
Lead Sponsor
PTC Therapeutics
INDUSTRY