The REPLACE Registry for Cholbam® (Cholic Acid)

Active, not recruitingOBSERVATIONAL
Enrollment

55

Participants

Timeline

Start Date

July 10, 2017

Primary Completion Date

July 31, 2038

Study Completion Date

July 31, 2039

Conditions
Bile Acid Synthesis Disorders
Interventions
DRUG

Cholbam

Cholbam prescribed according to the approved label.

Trial Locations (23)

10029

Icahn School Of Medicine at Mount Sinai, New York

10032

Montefiore Medical Center, New York

14642

Golisano Children's Hospital, URMC, Rochester

19104

The Children's Hospital of Philadelphia, Philadelphia

27599

UNC Chapel Hill, Chapel Hill

30329

Children's Healthcare of Atlanta, Atlanta

30342

Children's Center For Digestive Health, Atlanta

32207

Nemours duPont Pediatrics Specialty Clinic, Jacksonville

33021

Kidz Pediatric Multispecialty Group, Hollywood

33155

Nicklaus Children's Hospital, Miami

35233

University of Alabama Birmingham, Birmingham

37232

Monroe-Carell Jr. Children's Hospital at Vanderbilt, Nashville

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

46571

The Community Health Clinic, Topeka

55454

University of Minnesota, Minneapolis

55902

Mayo Clinic, Rochester

63110

Washington University at St Louis, St Louis

65201

Office of Dr. Esperanza Font-Montgomery MD, Columbia

70121

Ochsner Hospital for Children, New Orleans

73104

University of Oklahoma, Oklahoma City

84113

Primary Children's Hospital, Salt Lake City

94158

UC San Francisco, San Francisco

94305

Stanford School of Medicine, Palo Alto

Sponsors
All Listed Sponsors
lead

Mirum Pharmaceuticals, Inc.

INDUSTRY