8
Participants
Start Date
January 31, 2015
Primary Completion Date
April 5, 2017
Study Completion Date
April 5, 2017
Sodium Valproate
Subjects will receive sodium valproate modified release 20mg/kg/day (maximum dose 2.0g/day) administered orally once daily for six months.
Rigshospitalet, Copenhagen
MRC Centre for Neuromuscular Diseases, London
University College, London
OTHER